WASKYRA

STN: BLA 125846
Proper Name: etuvetidigene autotemcel
Tradename: WASKYRA
Manufacturer: Fondazione Telethon ETS
Indications:

Ttreatment of pediatric patients aged 6 months and older and adults with Wiskott-Aldrich Syndrome (WAS) who have a mutation in the WAS gene for whom hematopoietic stem cell transplantation (HSCT) is appropriate and no suitable human leukocyte antigen (HLA)-matched related stem cell donor is available.

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