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STN: 125755
Proper Name: elivaldogene autotemcel
Tradename: SKYSONA
Manufacturer: bluebird bio, Inc.

  • To slow the progression of neurologic dysfunction in boys 4-17 years of age with early, active cerebral adrenoleukodystrophy (CALD).

Product Information

  • Package Insert - SKYSONA
  • Demographic Subgroup Information – elivaldogene autotemcel [SKYSONA]
    Refer to Section 1.1 of the Clinical Review Memo for information about participation in the clinical trials and any analysis of demographic subgroup outcomes that is notable.

Supporting Documents

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