GENGLYCOS
STN:125858
Proper Name: pariglasgene brecaparvovec-opnr
Trade Name: GENGLYCOS
Manufacturer: Ultragenyx Pharmaceutical Inc.
- Indicated to reduce daily cornstarch intake as an adjunct to nutritional management in adult and pediatric patients 8 years of age and older with glycogen storage disease type Ia (GSDIa). This indication is approved under accelerated approval based on reduction in daily cornstarch intake. Continued approval for this indication may be contingent upon verification of clinical benefit in confirmatory trial(s).