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In this section: Cellular & Gene Therapy Products

LENMELDY

STN: 125758
Proper Name: atidarsagene autotemcel
Trade Name: LENMELDY
Manufacture: Orchard Therapeutics (Europe) Limited
Indication:

Indicated for the treatment of children with pre-symptomatic late infantile (PSLI), pre-symptomatic early juvenile (PSEJ) or early symptomatic early juvenile (ESEJ) metachromatic leukodystrophy (MLD)

Product Information

Package Insert - LENMELDY
Demographic Subgroup Information – atidarsagene autotemcel (LENMELDY)
Refer to Section 1.1 of the Clinical Review Memo for information about participation in the clinical trials and any analysis of demographic subgroup outcomes that is notable.

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