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- FDA Presentation: Additional Safeguards for Children in Research and Protocol Review Under 21 CFR 50.54
- Sponsor Presentation
- Parent and Patient Presentation: The Patient and Parent Perspective
- UCLA IRB Presentation: UCLA IRB FDA Referral on the Essence Trial for Duchenne Muscular Dystrophy
- UCLA Principal Investigator Presentation: The Essence Clinical Trial: Protocol Design and Obstacles