Learn About Expanded Access and Other Treatment Options
When a patient does not respond to current approved treatments for a variety of reasons, other options still may be available. For serious and life-threatening illnesses, some patients may want to talk to their healthcare provider about (1) trying an investigational drug through a clinical trial, expanded access, or right to try, or (2) trying an approved drug that is used for a different purpose than what is listed on the FDA-approved drug label (known as off-label use).
Understanding Unapproved Use of Approved Drugs "Off-Label"
Has your healthcare provider ever talked to you about using a drug to treat your disease or medical condition that has not been studied on patients with your disease? It maybe helpful for you to understand what "Off-Label" use means and the questions you may need to ask your healthcare provider.
Understanding Investigational Drugs
Has your healthcare provider ever talked to you about using an investigational drug to treat your disease or medical condition. It maybe helpful for you to understand what an investigational drug is before deciding if one might be right for you. Learn the basics of what they are and how you can get access.
Understanding Expanded Access (Compassionate Use)
Information about FDA's current expanded access policies, requirements for enrolling in expanded access programs, and steps you can take to get more information.
Understanding Right to Try
The Right to Try Act, or the Trickett Wendler, Frank Mongiello, Jordan McLinn, and Matthew Bellina Right to Try Act, was signed into law May 30, 2018. This law is another way for patients who have been diagnosed with life-threatening diseases or conditions who have tried all approved treatment options and who are unable to participate in a clinical trial to access certain unapproved treatments.