The resources below are intended as educational recordings about Orphan Products Natural History Grant Program. The table below identifies the intended audience for each of the topics, however these educational resources are meant to serve as a beneficial tool to all rare disease stakeholders.
|Recorded Session Topic||Patients & Advocacy Groups||Research Investigators||Drug Developers|
|Workshop on Natural History Studies in Rare Diseases: Meeting the Needs of Drug Development and Research
Gayatri Rao, JD, MD, OOPD; Richard Klein, OHCA; Charles "Tim" Frost, Patient, Alpha-1 Antitrypsin Deficiency; Gayle Greene, MSW, Caregiver, Von Hippel-Lindau Syndrome; Theresa Strong, PhD, Foundation for Prader-Willi Research; Andrew Mulberg, MD, FAAP, CDER/FDA; Jonathan Goldsmith, MD, FACP, CDER-Rare Disease Program/FDA