Information for Patients
Information for Patient Organizations
- The Division strives to create an open environment for discussion and collaboration with the patient community. Parties interested in working with the Division should contact the Division or Rare Diseases Program Group. Current efforts and prior examples of collaborative ventures can be found on the Meetings and Workshops page.
Information for Investigators and Industry
- Developing Products for Rare Diseases & Conditions
- Physician Request for a Single Patient IND for Compassionate or Emergency Use
- Investigator-Initiated Investigational New Drug (IND) Applications
- Guidance documents