1

 

                DEPARTMENT OF HEALTH AND HUMAN SERVICES

 

                      FOOD AND DRUG ADMINISTRATION

 

                CENTER FOR DRUG EVALUATION AND RESEARCH

 

 

 

 

 

 

 

 

 

 

 

 

 

                    DRUG SAFETY AND RISK MANAGEMENT

 

                       ADVISORY COMMITTEE (DSaRM)

 

                           COMMITTEE MEETING

 

 

 

 

 

 

 

 

 

 

 

 

 

 

                         Wednesday, May 5, 2004

 

                               8:18 a.m.

 

 

 

 

 

 

 

 

 

                CDER Advisory Committee Conference Room.

                           5630 Fishers Lane

                          Rockville, Maryland

                                                                 2

 

                        P A R T I C I P A N T S

 

      DSaRM Committee Members:

 

      Peter A. Gross, M.D., Chair

      Shalini Jain, PA-C, M.B.A., Executive Secretary

 

      Michael R. Cohen, R.Ph., M.S., D.Sc.

      Stephanie Y. Crawford, Ph.D., M.P.H.

      Curt D. Furberg, M.D., Ph.D.

      Jacqueline S. Gardner, Ph.D. M.P.H.

      Arthur A. Levin, M.P.H.

      Henri R. Manasse, Jr., Ph.D.

      Robyn S. Shapiro, J.D.

      Annette Stemhagen, Dr.PH

      Brian L. Strom, M.D., M.P.H.

 

      GI Advisory Committee Members:

 

      Alexander H. Krist, M.D.

      Maria H. Sjogren, M.D.

 

      Consultant:

 

      Leslie Hendeles, Pharm.D.

 

      FDA Participants:

 

      Carol Holquist, R.Ph.

      Marci Lee, Pharm.D.

      Paul Seligman, M.D., M.P.H. [a.m. and p.m.]

      Vibhakar Shah, Ph.D.

      Eugene Sullivan, M.D.

 

      Mark Avigan, M.D., C.M.

      Julie Beitz, M.D.

      Robert Justice, M.D., M.S.

      Ann Marie Trentacosti, M.D.

                                                                 3

 

                            C O N T E N T S

      AGENDA ITEM                                             PAGE

 

      Call to Order and Opening Remarks, Introduction of

      Committee - Peter Gross, M.D., Chair, DSaRM                5

 

      Conflict of Interest Statement - Shalini Jain,

      PA-C, M.B.A., Executive Secretary, DSaRM                   8

 

      Opening Remarks - Paul Seligman, M.D., M.P.H.,

      Director, Office of Pharmacoepidemiology &

      Statistical Science (OPSS) and Acting Director,

      Office of Drug Safety (ODS)                               11

 

      FDA Presentations

 

      - Permeability of LDPE Vials:  A Clinical

        Perspective - Eugene Sullivan, M.D., Deputy

        Director, Division of Pulmonary Drug Products.          13

      - Medication Errors and Low-Density Polyethylene

        (LDPE) Plastic Vials - Marci Lee, Pharm.D.,

        Safety Evaluator, Division of Medication Errors

        and Technical Support                                   23

      - LDPE Vials for Inhalation Drug Products:  A

        Chemistry, Manufacturing, and Controls (CMC)

        Perspective - Vibhakar Shah, Ph.D., Chemist,

        Division of New Drug Chemistry II                       36

 

      Questions from Committee                                  55

 

      Industry Presentations

 

      - Container Labeling Options using rommelag Blow-

        Fill-Seal Technology - Mohammad Sadeghi, V.P.,

        Research/Development, Holopack International

        Corp.                                                   65

      - Labeling of LDPE Containers:  Options for

        Improving Identification for Prevention of

        Medication Errors - Rick Schindewolf, V.P. & GM,

        Biotechnology & Sterile Life Sciences, and

        Patrick Poisson, Director of Technical Services,

        Biotechnology & Sterile Life  Sciences, Cardinal

        Health                                                  90

      - American Association of Respiratory Therapy

        Care - Karen Stewart, M.S., R.R.T.                      93

 

      Questions from Committee                                  94

                                                                 4

 

                      C O N T E N T S (Continued)

 

      Open Public Hearing                                      106

 

      Introduction of LDPE Issues

                Paul Seligman, M.D., M.P.H.                    118

 

      Committee Discussion                                     118

 

      Committee Discussion (Continued)                         182

 

      Opening Remarks and Reintroduction of Advisory

      Committee - Peter Gross, M.D., Chair                     182

 

      Conflict of Interest Statement - Shalini Jain,

      PA-C., M.B.A.                                            185

 

      Introduction of Lotronex Issue - Paul Seligman,

      M.D., M.P.H.                                             187

 

      Open Public Hearing                                      189

 

      Sponsor Presentation

 

      Risk Management Program for Lotronex - Craig Metz,

      Ph.D., V.P., U.S. Regulatory Affairs,

      GlaxoSmithKline                                          206

 

      FDA Presentation

 

      Lotronex Update - Robert Justice, M.D., M.S.,

      Director, Division of Gastrointestinal and

      Coagulation Drug Products                                241

 

      Questions from Committee                                 248

 

      Adjourn                                                  298

 

                                                                 5

 

  1                      P R O C E E D I N G S

 

  2             DR. GROSS:  Good morning.  I'm Peter

 

  3   Gross.  I'm Chair of the Drug Safety and Risk

 

  4   Management Committee, and starting with the person

 

  5   at my left with that famous laugh, Brian Strom,

 

  6   would you please introduce yourself?

 

  7             DR. STROM:  Thank you.  I'm Brian Strom

 

  8   from the University of Pennsylvania.

 

  9             MS. JAIN:  You know what?  Before we go

 

 10   on, Brian, Peter and the rest of the committee as

 

 11   well as the division wanted to say a warm thank-you

 

 12   for serving on our committee.  You've been a great

 

 13   asset for a year and a half, and we realize that

 

 14   you're going to continue as consultant, and we just

 

 15   wanted to say thanks.

 

 16             DR. STROM:  It's been a real pleasure, and

 

 17   it was a hard decision to let the rotation happen.

 

 18   I've enjoyed it, but given other commitments back

 

 19   home--but it's been fun.

 

 20             MS. JAIN:  Thank you.

 

 21             DR. GROSS:  You've been great, Brian.  We

 

 22   will continue to take advantage of your skills.

 

                                                                 6

 

  1             DR. MANASSE:  My name is Henri Manasse.

 

  2   I'm chief executive officer and executive vice

 

  3   president of the American Society of Health-System

 

  4   Pharmacists, a membership organization that

 

  5   represents about 32,000 pharmacists practicing in

 

  6   hospitals and organized health systems.

 

  7             MS. SHAPIRO:  Robyn Shapiro.  I'm a

 

  8   professor and director of the Center for the Study

 

  9   of Bioethics at the Medical College of Wisconsin.

 

 10             DR. STEMHAGEN:  I'm Annette Stemhagen.

 

 11   I'm Vice President of Strategic Development at

 

 12   Covance, a contract research organization, and I

 

 13   serve as an industry representative to this

 

 14   committee.

 

 15             DR. GARDNER:  Jacqueline Gardner,

 

 16   University of Washington, Department of Pharmacy.

 

 17             MR. LEVIN:  Art Levin, Center for Medical

 

 18   Consumers, and I serve as the consumer

 

 19   representative.

 

 20             DR. FURBERG:  Curt Furberg, professor of

 

 21   public health sciences at the Wake Forest

 

 22   University.

 

                                                                 7

 

  1             DR. HENDELES:  I'm Leslie Hendeles.  I'm a

 

  2   clinical pharmacist at the University of Florida,

 

  3   and I've done research on the bronchospastic

 

  4   effects of preservatives in nebulizer solutions.

 

  5             DR. CRAWFORD:  Good morning.  Stephanie

 

  6   Crawford, associate professor, College of Pharmacy,

 

  7   University of Illinois at Chicago.

 

  8             DR. COHEN:  Mike Cohen, Institute for Safe

 

  9   Medication Practices.

 

 10             DR. SELIGMAN:  Paul Seligman, Director,

 

 11   Office of Pharmacoepidemiology and Statistical

 

 12   Science, Center for Drug Evaluation and Research,

 

 13   FDA.

 

 14             DR. SULLVAN:  My name is Gene Sullivan.

 

 15   I'm the Deputy Director of the Division of

 

 16   Pulmonary and Allergy Drug Products here at FDA.

 

 17             MS. HOLQUIST:  I'm Carol Holquist.  I'm

 

 18   the Director of the Division of Medication Errors

 

 19   and Technical Support in the Office of Drug Safety,

 

 20   Center for Drug Evaluation and Research.

 

 21             DR. LEE:  Marci Lee, a pharmacist and

 

 22   safety evaluator in the Division of Medication

 

                                                                 8

 

  1   Errors and Technical Support.

 

  2             MS. JAIN:  Thank you, everyone.  My name

 

  3   is Shalini Jain.  I'm the Executive Secretary for

 

  4   the Drug Safety and Risk Management Advisory

 

  5   Committee.  I'll now read the conflict of interest

 

  6   statement for the meeting today.  The meeting issue

 

  7   is low-density polyethylene vials.

 

  8             The following announcement addresses the

 

  9   issue of conflict of interest with respect to this

 

 10   meeting and is made a part of the record to

 

 11   preclude even the appearance of such at this

 

 12   meeting.

 

 13             Based on the agenda, it has been

 

 14   determined that the topics of today's meeting are

 

 15   issues of broad applicability, and there are no

 

 16   products being approved at this meeting.  Unlike

 

 17   issues before a committee in which a particular

 

 18   product is discussed, issues of broader

 

 19   applicability involve many industrial sponsors and

 

 20   academic institutions.

 

 21             All special government employees have been

 

 22   screened for their financial interests as they may

 

                                                                 9

 

  1   apply to the general topics at hand.  To determine

 

  2   if any conflict of interest existed, the agency has

 

  3   reviewed the agenda and all relevant financial

 

  4   interests reported by the meeting participants.

 

  5   The Food and Drug Administration has granted

 

  6   general matters waivers to the special government

 

  7   employees participating in this meeting who require

 

  8   a waiver under Title 18, United States Code,

 

  9   Section 208.

 

 10             A copy of the waiver statements may be

 

 11   obtained by submitting a written request to the

 

 12   agency's Freedom of Information Office, Room 12A-30

 

 13   of the Parklawn Building.

 

 14             Because general topics impact so many

 

 15   entities, it is not prudent to recite all potential

 

 16   conflicts of interest as they apply to each member,

 

 17   consultants, and guest speaker.

 

 18             FDA acknowledges that there may be

 

 19   potential conflicts of interest, but because of the

 

 20   general nature of the discussion before the

 

 21   committee, these potential conflicts are mitigated.

 

 22             With respect to FDA's invited industry

 

                                                                10

 

  1   representative, we would like to disclose that Dr.

 

  2   Annette Stemhagen is participating in this meeting

 

  3   as an industry representative, acting on behalf of

 

  4   regulated industry.  Dr. Stemhagen is employed by

 

  5   Covance Periapproval Services, Incorporated.

 

  6             In addition, we would like to note that

 

  7   Karen Stewart, FDA's invited guest speaker, is

 

  8   participating as a representative of the

 

  9   respiratory therapists in the United States through

 

 10   the American Association for Respiratory Care.  She

 

 11   has no financial interest in or professional

 

 12   relationship with any of the products or firms that

 

 13   could be affected by the committee's discussions.

 

 14             With respect to the three invited industry

 

 15   guest speakers, we would like to disclose that

 

 16   Mohammad Sadeghi is employed by Holopack

 

 17   International,  Richard Schindewolf is employed by

 

 18   Cardinal Health and is vice president and general

 

 19   manager of Biotechnology and Sterile Life Sciences.

 

 20   Patrick Poisson is employed by Cardinal Health, and

 

 21   he serves as Director of Technical Services at the

 

 22   Biotechnology and Sterile Life Sciences division.

 

                                                                11

 

  1             In the event that the discussions involve

 

  2   any other products or firms not already on the

 

  3   agenda for which FDA participants have a financial

 

  4   interest, the participants' involvement and their

 

  5   exclusion will be noted for the record.

 

  6             With respect to all other participants, we

 

  7   ask in the interest of fairness that they address

 

  8   any current or previous financial involvement with

 

  9   any firm whose product they may wish to comment

 

 10   upon.

 

 11             Thank you.

 

        x                   DR. SELIGMAN:  Good morning.  On behalf of         

   12

 

 13   the Center for Drug Evaluation and Research, it is

 

 14   my pleasure to welcome members of the Drug Safety

 

 15   and Risk Management Advisory Committee and members

 

 16   of the public to today's meeting.  As always, we

 

 17   greatly appreciate the time and efforts devoted by

 

 18   the committee members and all participants in

 

 19   providing advice to the FDA on important public

 

 20   health issues.

 

 21             We have two topics on the agenda for

 

 22   discussion today--the first related to the

 

                                                                12

 

  1   prevention of medication errors and the second

 

  2   providing an update on a risk management program

 

  3   that was considered by this committee two years ago

 

  4   and was implemented in 2002.

 

  5             The first topic will focus primarily on

 

  6   minimizing the incidence of medication errors with

 

  7   drug products packages in low-density polyethylene,

 

  8   or LDPE, containers.  The package is intended to

 

  9   preserve drug product purity and quality.  However,

 

 10   current techniques used to label the product create

 

 11   problems related to legibility of the product name

 

 12   and strength.  Additionally, various products are

 

 13   packaged in containers that look similar.  We've

 

 14   found that these difficult-to-read labels and

 

 15   look-alike containers have contributed to

 

 16   medication errors involving the administration of

 

 17   wrong dosage strength or wrong drug product to the

 

 18   patient.

 

 19             Today, we would like to discuss what other

 

 20   solutions or alternative packaging designs exist

 

 21   that could improve the legibility of the label,

 

 22   prevent ingress of chemical contaminants, and in

 

                                                                13

 

  1   the process reduce or eliminate medication errors.

 

  2   Then later this afternoon, we will receive an

 

  3   update on the Lotronex risk management program.

 

  4             With that brief introduction, I look

 

  5   forward to our discussions today and, again, I also

 

  6   want to personally thank Dr. Strom for his service

 

  7   on this committee.

 

  8             With that, I guess we may proceed with the

 

  9   first speaker.  Dr. Gross?

 

 10             DR. GROSS:  Dr. Sullivan will be the first

 

 11   speaker on the Permeability of LDPE Vials:  A

 

 12   Clinical Perspective.

 

 13             DR. SULLIVAN:  Good morning.  As I

 

 14   mentioned, my name is Gene Sullivan.  By training

 

 15   I'm a pulmonologist, and I'm the Deputy Director of

 

 16   the Division of Pulmonary and Allergy Drug Products

 

 17   in the Center for Drug Evaluation and Research here

 

 18   at FDA.

 

 19             This morning, I'm going to spend about 15

 

 20   minutes or so providing some background for the

 

 21   discussions today.  I'll be conveying some clinical

 

 22   observations regarding issues raised by the use of

 

                                                                14

 

  1   LDPE vials in the packaging of inhalation drug

 

  2   products, particularly as it relates to the

 

  3   permeability of the vials.

 

  4             This slide provides an overview of my

 

  5   presentation.  I'll begin with some introductory

 

  6   remarks which will put my presentation into the

 

  7   context of today's discussions and will serve to

 

  8   introduce the remainder of the talk.  Next I will

 

  9   discuss the inhalation drug products that are

 

 10   involved, providing some examples and a brief

 

 11   description of the nature of these drugs.

 

 12   Following this, I will discuss the patient

 

 13   populations for which these drugs are used,

 

 14   emphasizing aspects of these populations that put

 

 15   them at risk for adverse effects of chemical

 

 16   contaminants.  Then I will discuss the potential

 

 17   sources of chemical contaminants, their potential

 

 18   adverse effects, and the difficulties that exist in

 

 19   terms of adequately monitoring for them.  Finally,

 

 20   I will summarize the issue and current state of

 

 21   affairs in order to set the stage for the remainder

 

 22   of today's discussion regarding minimizing the

 

                                                                15

 

  1   potential for medication errors.

 

  2             The topic for discussion for today's

 

  3   Advisory Committee meeting is how best to minimize

 

  4   the potential for medication errors associated with

 

  5   LDPE containers, particularly given the clinical

 

  6   concerns related to their permeability and the

 

  7   resulting move away from the paper labels that have

 

  8   previously been used to identify the products.  My

 

  9   presentation is intended to review the nature of

 

 10   these clinical concerns in order to provide

 

 11   background for the remainder of the discussions

 

 12   today.

 

 13             This slide summarizes the clinical

 

 14   concerns that I mentioned.  Many inhalation drug

 

 15   products are packaged in LDPE containers.  LDPE is

 

 16   a material that is permeable to volatile chemicals,

 

 17   and there are numerous volatile chemicals that

 

 18   exist in the immediate packaging environment.

 

 19   Volatile chemicals that find their way into

 

 20   inhalation solutions may have a number of adverse

 

 21   effects on the airways, and because these adverse

 

 22   effects may be poorly tolerated by patients,

 

                                                                16

 

  1   efforts should be made to minimize the potential

 

  2   for contamination of inhalation drug products.

 

  3   Such efforts have included minimizing the content

 

  4   of volatile chemicals in the immediate packaging

 

  5   environment.

 

  6             For instance, the practice of using paper

 

  7   labels, which are applied directly to the LDPE

 

  8   containers and which contain numerous volatile

 

  9   chemicals, is not recommended.  However, as you

 

 10   will see in subsequent presentations, the use of

 

 11   alternative labeling approaches has raised the

 

 12   issue of medication errors.

 

 13             Now, I also want to point out that my

 

 14   presentation is focused on the clinical concerns

 

 15   related to chemical contamination of these

 

 16   products.  In the next presentation, Dr. Shah will

 

 17   also talk about product quality concerns.  For

 

 18   instance, ingress of volatile chemicals might

 

 19   adversely affect the stability of the active drug

 

 20   substance in a particular drug product.

 

 21             This slide provides some examples of

 

 22   inhalation drug products that are packaged in LDPE

 

                                                                17

 

  1   containers.  They include bronchodilators, such as

 

  2   Albuterol, Ipatropium, Metaproterenol, and

 

  3   Levalbuterol; also a mass cell stabilizer, cromolyn

 

  4   sodium; an inhaled steroid, Budesonide; and an

 

  5   antibiotic, Tobramycin.

 

  6             These products are inhalation solutions,

 

  7   or sometimes suspensions, that are intended for

 

  8   oral inhalation using a nebulizer.  One thing to

 

  9   keep in mind is that the manufacturing processes

 

 10   and materials for inhalation products are very

 

 11   carefully controlled in order to maintain a very

 

 12   high standard of product purity.  That is, a

 

 13   significant amount of attention is paid to the

 

 14   manufacturing processes and the materials used so

 

 15   that the content of contaminants is minimized.

 

 16   This would include contaminants that arise during

 

 17   the manufacturing processes, so-called process of

 

 18   synthetic impurities; contaminants that arise due

 

 19   to degradation of components of the formulation; or

 

 20   the subject of today's concern, contaminants that

 

 21   enter the formulation from the packaging materials,

 

 22   so-called leachables.

 

                                                                18

 

  1             These drugs may be used in a regular

 

  2   dosing schedule or may be used as an as-needed

 

  3   basis, and the bronchodilator products in

 

  4   particular are common used in the inpatient and

 

  5   acute-care settings, including emergency

 

  6   departments and intensive care units.

 

  7             These inhalation products are used by

 

  8   patients with a variety of pulmonary disorders,

 

  9   most commonly patients with asthma, COPD--which is

 

 10   chronic obstructive pulmonary disease, a category

 

 11   of lung disease comprised of chronic bronchitis and

 

 12   emphysema--and cystic fibrosis.  Although these

 

 13   diseases are distinct, in general they are

 

 14   characterized by fixed or variable obstruction to

 

 15   airflow and a variety of patterns of histologic

 

 16   abnormalities, including various patterns of airway

 

 17   inflammation.  In addition, asthma in particular is

 

 18   associated with an underlying propensity for

 

 19   allergic responses.  And most of the diseases are

 

 20   associated with a sensitivity to nonspecific

 

 21   irritants which result in acute bronchospasm, a

 

 22   feature known as airway hyperresponsiveness.

 

                                                                19

 

  1             To focus specifically on asthmatics for a

 

  2   moment, asthmatics may react adversely to both

 

  3   nonspecific chemical irritants and to allergens to

 

  4   which they have developed specific immunity.

 

  5   Irritant reactions are characterized by symptoms of

 

  6   wheezing and shortness of breath.  It is well known

 

  7   that patients with severe asthma may react to very

 

  8   low levels of exposure to irritants.  Clinically,

 

  9   this is often related to perfumes, cleaning agents,

 

 10   or smoke in the environment.  In fact, we commonly

 

 11   make use of this feature of asthma to help

 

 12   establish the diagnosis using methacholine

 

 13   challenge testing.  In the methacholine challenge

 

 14   test, patients with suspect asthma are exposed to

 

 15   successively higher concentrations of this irritant

 

 16   in order to elicit bronchospasm.

 

 17             In addition to the nonspecific irritant

 

 18   reactions, asthmatics may also develop bronchospasm

 

 19   from inhaled allergens.  This allergic reaction is

 

 20   associated with both an acute early-phase broncho-

 

 21   constriction and a delayed late-phase response

 

 22   characterized by airway inflammation and airflow

 

                                                                20

 

  1   limitation.

 

  2             So what are the potential sources of

 

  3   contaminants in inhalation drug products packaged

 

  4   in LDPE?  In general, these are from volatile

 

  5   chemicals found in the labels and secondary bulk

 

  6   packaging.  These chemicals may be found in the

 

  7   various glues, inks, and lacquers that are used.

 

  8   One thing to point out is that the specific

 

  9   chemical nature of these inks, glues, et cetera,

 

 10   may, in fact, change after approval due to changes

 

 11   in the sources of these packaging materials.

 

 12             The FDA conducted an analytical survey of

 

 13   approved inhalation solutions marketed in LDPE

 

 14   containers and found that 29 of the 37 samples

 

 15   tested positive for various volatile chemicals that

 

 16   were presumed to have originated in the packaging

 

 17   materials.  Dr. Shah will describe this analysis in

 

 18   much more detail in his presentation later this

 

 19   morning.

 

 20             Chemical contaminants in inhalation drug

 

 21   products may be associated with a variety of

 

 22   adverse effects, including irritant and immunologic

 

                                                                21

 

  1   effects, leading to acute bronchospasm and airway

 

  2   inflammation and hyperresponsiveness, other toxicologic

 

  3   injury, or even potentially carcinogenicity.

 

  4             In terms of monitoring for adverse effects

 

  5   that might be attributed to chemical contaminants

 

  6   in these products, it is important to note that

 

  7   appropriate attribution may be very difficult

 

  8   because the expected adverse effects--bronchospasm

 

  9   and airway hyperresponsiveness--mimic the symptoms

 

 10   for which the drugs are being used.  This is a very

 

 11   difficult circumstance and makes it quite likely

 

 12   that adverse effects would not be recognized and

 

 13   reported.  For instance, modest bronchospasm

 

 14   related to chemical contaminants might lead to

 

 15   reduced efficacy of the drug, but this would likely

 

 16   not be identified.  Even if the adverse effect were

 

 17   more significant, the findings would likely be

 

 18   attributed to refractory underlying disease.

 

 19             So, to summarize, many inhalation drug

 

 20   products are packaged in low-density polyethylene

 

 21   containers.  This material is permeable to volatile

 

 22   chemicals.  Numerous volatile chemicals exist in

 

                                                                22

 

  1   the immediate packaging environment.

 

  2             Various volatile chemicals have, in fact,

 

  3   been identified in these products.  These volatile

 

  4   chemicals may have irritant as well as other

 

  5   toxicologic effects.  And because these effects may

 

  6   be particularly poorly tolerated by patients,

 

  7   efforts should be made to minimize the potential

 

  8   for contamination of inhalation drug products.

 

  9             It was this line of reasoning that in part

 

 10   led to the development of the Draft Guidance

 

 11   entitled "Inhalation Drug Products Packaged in

 

 12   Semipermeable Container Closure Systems."  Among

 

 13   other things, the Draft Guidance recommends that

 

 14   measures be taken to limit chemical contamination

 

 15   of these products.  One such measure would be the

 

 16   use of alternative approaches to paper labels, such

 

 17   as direct embossing or debossing of the containers.

 

 18             However, as will be discussed in

 

 19   subsequent presentations, the move away from paper

 

 20   labels has introduced a new concern, that of

 

 21   medication errors due to difficult-to-read and

 

 22   look-alike packaging.  The issue of how best to

 

                                                                23

 

  1   minimize the potential for medication errors will

 

  2   be the topic for today's discussion.

 

  3             DR. GROSS:  Thank you, Dr. Sullivan.

 

  4             The next speaker will be Shah.

 

  5             MS. JAIN:  He is not here.

 

  6             DR. GROSS:  Okay.  Later for Dr. Shah.

 

  7             Dr. Marci Lee will now talk about

 

  8   medication errors and low-density polyethylene

 

  9   plastic vials.

 

 10             DR. LEE:  Good morning.  My name is Marci

 

 11   Lee.  I am a pharmacist and safety evaluator in the

 

 12   Division of Medication Errors and Technical Support

 

 13   in the Office of Drug Safety.

 

 14             The purpose of this presentation is to

 

 15   describe medication error reports and feedback from

 

 16   patients and practitioners involving products

 

 17   packaged in LDPE containers.  I will focus on some

 

 18   factors we identified that may contribute to

 

 19   confusion and errors with these products.  Finally,

 

 20   I will describe packaging and labeling approaches

 

 21   for your consideration.

 

 22             Our error analysis included in your

 

                                                                24

 

  1   background package was from 87 relevant reports.

 

  2   These came from patients, caregivers, and

 

  3   practitioners, such as respiratory therapists and

 

  4   pharmacists, who reported to the programs listed.

 

  5   These reports were received between January 1993

 

  6   and August 2002.  Many reports involved difficulty

 

  7   reading embossed product containers.  Some reports

 

  8   were actual errors where the wrong medication or

 

  9   the wrong dosage strengths were dispensed.

 

 10   Although some of these were detected before the

 

 11   medication was administered to the patient, some

 

 12   were not.  The outcomes of these reports ranged

 

 13   from no harm to difficulty breathing, which can be

 

 14   life-threatening.  The remainder of the reports

 

 15   described the potential for confusion and errors

 

 16   with these products.  Subsequently, as of April

 

 17   2004, 51 additional relevant medication error

 

 18   reports were identified for a total of 138 reports.

 

 19             In addition to our analysis, FDA received

 

 20   correspondence from ISMP, USP, and Senator Harkin

 

 21   regarding the safe use of products packaged in LDPE

 

 22   containers.

 

                                                                25

 

  1             Several themes emerged from the narratives

 

  2   of the medication error reports as factors that can

 

  3   contribute to errors.  They include

 

  4   difficult-to-read containers, look-alike packaging,

 

  5   and routine handling of LDPE by patients and health

 

  6   care practitioners.

 

  7             Some of the slides for this portion of the

 

  8   presentation will include direct quotes from the

 

  9   error reporters.  The first contributing factor to

 

 10   consider is the difficult-to-read labeling.

 

 11   Concern was expressed in a medication error report

 

 12   because it is difficult to see the name of the drug

 

 13   and its ingredients.  Another person noted that if

 

 14   the lot and expiration date are on opposite sides

 

 15   of the same area of plastic, it is even more

 

 16   difficult to read.  In addition, practitioners

 

 17   described how the vials needed to be angled in the

 

 18   light to read them.  For some, the text is

 

 19   difficult or impossible to read.

 

 20             In addition to difficult-to-read

 

 21   containers, another concern from the medication

 

 22   error perspective is the issue of look-alike

 

                                                                26

 

  1   packaging.  Often there is very little on the

 

  2   container itself to help people distinguish these

 

  3   products.

 

  4             This photo accompanied one medication

 

  5   error report.  It highlights the potential for

 

  6   confusion from look-alike vials from just a few of

 

  7   the products available in these containers.  Almost

 

  8   all of these vials contain a different drug

 

  9   product.  The paper labels and the unique round

 

 10   vial shape help to differentiate three of the vials

 

 11   from the rest.  However, these two can be difficult

 

 12   to read.

 

 13             In addition, this problem spans various

 

 14   drug classes and routes of administration.  This

 

 15   complicates the picture for practitioners and

 

 16   creates the opportunity for errors to occur among

 

 17   inhalation, injection, ophthalmic, and oral

 

 18   products.

 

 19             In this case, heparin is an injectable

 

 20   medication.  This photo was included with the

 

 21   report of potential for confusion between heparin

 

 22   and Tobramycin due to look-alike containers. 

 

                                                                27

 

  1   Pharmacies may store a variety of these products,

 

  2   and the potential for confusion will likely

 

  3   increase as we see more products other than

 

  4   inhalation solutions packaged in the LDPE

 

  5   containers.  This increases the likelihood for

 

  6   administration of the wrong drug product by the

 

  7   wrong route of administration.

 

  8             Another example of an injectable drug

 

  9   product with similar packaging is Naropin.  These

 

 10   ampules are specially design to fit both Luer lock

 

 11   and Luer slip syringes.  Although this feature may

 

 12   minimize the likelihood for confusion with the

 

 13   other LDPE containers, there is still potential for

 

 14   confusion between the dosage strengths within the

 

 15   Naropin product line.  This vial includes black

 

 16   type on a clear background.  Again, for some this

 

 17   may be difficult to read.

 

 18             Timoptic OCUDOSE is an example of an

 

 19   ophthalmic solution packaged in an LDPE container.

 

 20   This image shows that the tip of the container has

 

 21   been extended to allow for a label.  However, there

 

 22   may be potential for contamination despite the

 

                                                                28

 

  1   placement of this label.

 

  2             Gastrocom is an example of a product for

 

  3   oral administration that is packaged in an LDPE

 

  4   container.  This image illustrates the instructions

 

  5   for use.

 

  6             In summary, there are least four different

 

  7   routes of administration for products packaged in

 

  8   LDPE containers.  Again, this complicates the

 

  9   picture for practitioners and creates the

 

 10   opportunity for errors to occur among inhalation,

 

 11   injection, ophthalmic, and oral drug products.

 

 12             We have discussed several issues that

 

 13   contribute to medication errors with LDPE

 

 14   containers.  We have seen examples of containers

 

 15   that are difficult to read and difficult to

 

 16   distinguish from one another.  We have noted that

 

 17   the look-alike contains look-alike containers are

 

 18   not from a single drug product category or

 

 19   associated with a single route of administration.

 

 20   Now we will explore how routine handling of LDPE

 

 21   containers by patients and practitioners can

 

 22   contribute to errors.

 

                                                                29

 

  1             The foil overwrap serves to protect the

 

  2   containers from light and the environment.  It is

 

  3   recommended that the containers are stored in the

 

  4   foil overwrap until time of use.  However, the

 

  5   reality is that the foil overwraps are commonly

 

  6   discarded.  Once discarded, the clearly labeled

 

  7   portion of the packaging is often eliminated.

 

  8             One reason noted in our analysis for the

 

  9   overwrap to be removed is an effort to fit the

 

 10   products into a medication cart.  The foil overwrap

 

 11   and carton for many inhalation solutions use color

 

 12   to differentiate the dosage strength.  Most foil

 

 13   overwraps contain multiple unit dose LDPE vials.

 

 14   For example, the foil overwrap for Xopenex contains

 

 15   12 vials.

 

 16             Carol, if you'll pass the sample?

 

 17             This image includes the 12 vials which are

 

 18   contents of a single foil pouch of Xopenex.  All of

 

 19   the vials in this image are the same dosage

 

 20   strength.  However, Xopenex is available in three

 

 21   different dosage strengths.  The vials for all

 

 22   three strengths look alike when they are removed

 

                                                                30

 

  1   from the foil.  Although the foil helps to

 

  2   differentiate them, it is possible that these vials

 

  3   may not remain in the foil pouch until their time

 

  4   of use.  These individual LDPE containers can be

 

  5   stored in a variety of places once removed from the

 

  6   foil overwrap.

 

  7             It is a common practice for LDPE

 

  8   containers to be stored in the pockets or pouches

 

  9   of the practitioners who administer these

 

 10   medications.  In summary, while it is possible for

 

 11   various products to have clearly marked foil

 

 12   overwraps, as long as the containers themselves are

 

 13   poorly marked there is still potential for

 

 14   confusion.

 

 15             Once the container leaves the foil

 

 16   overwraps, it no longer matters how well labeled

 

 17   the foil pouch is.  This is a concern, regardless

 

 18   of the number of vials contained in the foil

 

 19   overwrap.  However, a single container in the foil

 

 20   pouch may minimize the likelihood for the vial to

 

 21   become separated from the overwrap.

 

 22             At this point we would like to stimulate

 

                                                                31

 

  1   ideas for discussion about how to address the

 

  2   issues that have been raised so far.  The remainder

 

  3   of this presentation will include a series of

 

  4   photos.  These images will highlight various

 

  5   packaging and labeling approaches to consider.

 

  6   Remember to keep in mind who will be using the

 

  7   products and how they will be used.  Our goal is to

 

  8   identify packaging that will resolve our concerns

 

  9   but not introduce any new problems for those who

 

 10   manufacture or use the products.

 

 11             The paper label approach allows for use of

 

 12   color to distinguish look-alike vials.  For some,

 

 13   these may difficult to read due to the small font

 

 14   size of the text.  The reports in our analysis

 

 15   demonstrated that some people may identify these

 

 16   medications by the color of their label alone.

 

 17   Based on the earlier presentation, we learned of

 

 18   the potential safety and product quality concerns

 

 19   with this approach for inhalation solutions.

 

 20             Although this packaging no longer appears

 

 21   to be used for Timoptic, this image illustrates

 

 22   another approach with paper labels.  The paper

 

                                                                32

 

  1   label is applied to the tip of the container.  The

 

  2   packaging allows for use of color to differentiate

 

  3   the containers and dosage strengths.  However, it

 

  4   may not address the potential for ingress.

 

  5             Again, consider the size of the label and

 

  6   the potential font size issues which may make the

 

  7   text difficult to read.

 

  8             We have a sample of this also going

 

  9   around.

 

 10             Here is an approach that extends the tip

 

 11   of the container to allow for the text to be

 

 12   embossed in the flange instead of the body of the

 

 13   vial.  This approach allows for more space for

 

 14   printed text; however, if both sides are embossed,

 

 15   they tend to interfere with the readability of the

 

 16   text.

 

 17             In contrast, this approach includes an

 

 18   embossed container without an extended flange.  In

 

 19   addition, the container is topped with the letter

 

 20   V-shaped tip.  In this case, V is for Ventolin.

 

 21   This approach allows for use of the unique vial

 

 22   shape and possibly texture to help differentiate

 

                                                                33

 

  1   the product.

 

  2             Another approach used to differentiate the

 

  3   various products in LDPE vials is the use of the

 

  4   embossed letters A, I, and R at the tip of the

 

  5   container.  In addition to a visual cue, the vial

 

  6   makes use of texture to distinguish the products.

 

  7   A is for Albuterol, I is for Ipatropium, and so on.

 

  8   Again, for some this is difficult to read.

 

  9             One approach that has contributed to

 

 10   medication errors with acetylcysteine is the use of

 

 11   a glass vial.  The packaging has led to medication

 

 12   errors where practitioners inject the product

 

 13   instead of administering the drug via inhalation

 

 14   because the vials look similar to those that

 

 15   contain an injectable product.  According to the

 

 16   May 30, 2001, ISMP newsletter article, these error

 

 17   occur despite warnings on the label that state "Not

 

 18   for injection" or "For inhalation."  In addition,

 

 19   they have a target area on the rubber stopper

 

 20   similar to the injectable products.

 

 21             Another approach used to distinguish these

 

 22   products includes the use of a uniquely shaped

 

                                                                34

 

  1   container.  Although these round vials distinguish

 

  2   Pulmicort from other drug products, it is difficult

 

  3   to differentiate between the two dosage strengths

 

  4   of Pulmicort once they are removed from the foil.

 

  5   The image on the right illustrates what the

 

  6   containers look like once the foil overwrap is

 

  7   removed.

 

  8             Some products, such as sodium chloride

 

  9   inhalation solution, utilize a tinted vial as a

 

 10   means of differentiation.  This approach allows for

 

 11   the use of color to help differentiate the

 

 12   containers from other products.  However, this

 

 13   particular packaging has not been evaluated by CDER

 

 14   at FDA.  These vials also include embossed text.

 

 15             Another approach is the shrink wrap

 

 16   approach which allows for the combination of

 

 17   embossed information on the end of the vial and the

 

 18   use of black print on a clear background.  Again,

 

 19   for some this may be difficult to read.  The

 

 20   printed portion of this label clings to the vials

 

 21   without adhesives, eliminating one potential source

 

 22   of packaging contamination.  However, there are

 

                                                                35

 

  1   still sources of volatile chemicals with the shrink

 

  2   wrap approach.

 

  3             There's also a sample of this going

 

  4   around.  The individual foil overwrap approach was

 

  5   described in the Draft Guidance that Dr. Sullivan

 

  6   referred to in his presentation.  This method will

 

  7   protect the drug product from contamination from

 

  8   the environment and minimize the opportunity for

 

  9   contamination from the packaging itself.

 

 10             Each foil overwrap contains a single vial.

 

 11   This is thought to increase the likelihood of the

 

 12   pouch staying with the container and minimize the

 

 13   risk for errors.  The overwrap allows for the use

 

 14   of color and other means of differentiation to help

 

 15   distinguish these products.

 

 16             At this time we are seeking other ideas

 

 17   and approaches to consider.  What other materials

 

 18   could we use?  What has been done for other

 

 19   products?  What will meet the needs of those using

 

 20   the products in both the inpatient and outpatient

 

 21   setting?  How should FDA evaluate any proposed

 

 22   changes?

 

                                                                36

 

  1             Also ask yourself, Will it prevent

 

  2   contamination from secondary packaging in the

 

  3   environment?  Will it be difficult to read?  Will

 

  4   it look like other containers?  Will it create new

 

  5   problems?  Will it be difficult to use?  And,

 

  6   finally, should inhalation products be handled

 

  7   separately from products with other routes of

 

  8   administration?  We look forward to hearing your

 

  9   ideas and suggestions.

 

 10             DR. GROSS:  Okay.  To round out the

 

 11   presentations, Dr. Shah will talk about the

 

 12   perspective for chemistry, manufacturing, and

 

 13   controls.

 

 14             DR. SHAH:  Good morning.  My name is

 

 15   Vibhakar Shah, and I'm a chemist in the Office of

 

 16   New Drug Chemistry for Pulmonary and Allergy Drug

 

 17   Products.  Before I start, I would like to

 

 18   apologize for my delay.  I was stuck in traffic for

 

 19   almost one and a half hours.  Let me tell you, it's

 

 20   not a pleasant experience.  But, in any case,

 

 21   that's life.  And I'm sure when we move to White

 

 22   Oak it's going to get worse.

 

                                                                37

 

  1             [Laughter.]

 

  2             DR. SHAH:  You were supposed to hear this

 

  3   talk before Marci's talk, but, anyway, here it

 

  4   goes.

 

  5             You already heard from Dr. Sullivan the

 

  6   clinical concerns arising due to the permeability

 

  7   of LDPE vials, especially when used with paper

 

  8   labels for inhalation drug products, and also you

 

  9   heard some of the medication errors which are

 

 10   caused because of legibility issues with the paper

 

 11   labels.  And I'm going to talk about in the next 20

 

 12   minutes regarding the problems and issues with

 

 13   product quality concerns arising due to the use of

 

 14   LDPE containers, with or without paper labels and

 

 15   with or without overwrap, for these drug products.

 

 16             In the context of today's discussion, my

 

 17   presentation will also focus on how best to

 

 18   minimize the potential medication errors given the

 

 19   quality concerns associated with these container

 

 20   closures.

 

 21             With that, this slide gives you the

 

 22   outline of my talk.  I'm going to start with a

 

                                                                38

 

  1   brief introduction to the type of inhalation drug

 

  2   products that are packaged in LDPE containers, and

 

  3   after that I'll be overviewing the current

 

  4   container-closure systems that are used.  Following

 

  5   that, I would like to discuss the results of an

 

  6   analytical survey conducted by the agency for

 

  7   several inhalation drug products under the Drug

 

  8   Product Quality Surveillance Program.  This survey

 

  9   particularly identified the clinical concerns as

 

 10   well as the quality concerns arising from the drug

 

 11   product contamination by packaging components

 

 12   because of the permeability of LDPE.

 

 13             Following that, I would like to discuss

 

 14   some of the quality concerns arising with the use

 

 15   of LDPE vials, with or without paper label and foil

 

 16   overwrap.  I will discuss the agency's current

 

 17   approaches to control and minimize the product

 

 18   contamination from packaging components and discuss

 

 19   current recommendations for packaging of inhalation

 

 20   drug products as provided in the Draft Guidance.

 

 21   And I will end my presentation with summarizing the

 

 22   quality concerns, what I have discussed so far.

 

                                                                39

 

  1             This slide lists the inhalation dosage

 

  2   forms administered by oral inhalation, and these

 

  3   drug products include inhalation solutions,

 

  4   suspensions, spray, inhalation aerosol, and

 

  5   inhalation powder.  However, for today's

 

  6   discussion, the remainder of the talk will focus on

 

  7   inhalation solutions and suspensions as they are

 

  8   the only two dosage forms that are packaged in LDPE

 

  9   containers.

 

 10             This slide you have already seen in Dr.

 

 11   Sullivan's presentation.  It just shows the type of

 

 12   drug products which are packaged into LDPE

 

 13   containers.

 

 14             Currently, inhalation solutions and

 

 15   suspensions are packaged in LDPE vials, and there

 

 16   are three components, basically:  LDPE vials, vial

 

 17   labels, and foil overwrap pouch.  Not all the

 

 18   inhalation solutions and suspensions may have foil

 

 19   overwrap pouch or adhesive paper label.  But in any

 

 20   case, the unit-dose vial--that is, the LDPE

 

 21   vial--is made up of low-density polyethylene by

 

 22   blow-fill-seal or form-fill-seal process.  The

 

                                                                40

 

  1   labeling information on a vial is conveyed either

 

  2   by a self-adhesive printed paper label or by

 

  3   embossing or debossing the labeling information on

 

  4   the LDPE vial itself during the fabrication of the

 

  5   vial.

 

  6             Foil overwrap acts as a protective

 

  7   secondary package and may contain anywhere from one

 

  8   to 12 vials per pouch.  The labeling information

 

  9   may be conveyed by a self-adhesive paper label on

 

 10   the foil overwrap, or the foil overwrap may be

 

 11   printed.  Furthermore, different colors for foil

 

 12   pouches may be used to differentiate the multiple

 

 13   strengths of the drug product.

 

 14             Now, let me go over the container-closure

 

 15   components of the LDPE vial, paper label, and

 

 16   foil-laminate.  I'll start the LDPE vial.

 

 17             The unit-dose vial, which is made up of

 

 18   low-density polyethylene, is chemically a

 

 19   polyethylene homo-polymer resin.  The polyethylene

 

 20   resin is made by polymerization process and may

 

 21   contain several chemical additives in addition to

 

 22   the reactant polymer.  They include chain transfer

 

                                                                41

 

  1   agent, chain initiator, antioxidant, so on and so

 

  2   forth.

 

  3             Furthermore, it is available in different

 

  4   grades for different applications.  That indicates

 

  5   that the composition of the LDPE may change

 

  6   depending upon how it is being used.  There are

 

  7   many manufacturers and suppliers of this LDPE.

 

        T1B                 This slide lists some of the               8

 

  9   characteristics and properties offered by LDPE or

 

 10   LDPE vials which probably makes it a material of

 

 11   choice for packaging of inhalation solution and

 

 12   suspensions from a manufacturer's point of view.

 

 13   These include:  they are flexible and malleable;

 

 14   stress crack, impact, and tear resistant; they are

 

 15   considered chemically inert at room temperature; or

 

 16   it may be used at elevated temperature for extended

 

 17   periods of time; or it can be sterilized.  They are

 

 18   used on high-speed production lines and,

 

 19   aesthetically, they can be clear to translucent in

 

 20   appearance.

 

 21             However, it is permeable to volatile

 

 22   chemicals and gases, and because of this

 

                                                                42

 

  1   permeability, there are several quality concerns

 

  2   which I'll be discussing later in my talk.

 

  3             The next I would like to talk about is the

 

  4   paper label, the components of a self-adhesive

 

  5   paper label and how it may contribute to the

 

  6   quality concerns of inhalation solutions and

 

  7   suspensions.

 

  8             Typically, a paper label consists of a

 

  9   base paper, adhesive, inks, pigments and dyes,

 

 10   varnishes, over-lacquer, et cetera, and depending

 

 11   upon the application, the base paper may contain or

 

 12   may be treated with all or many of the chemicals

 

 13   that I have listed here.

 

 14             Adhesive is the layer which comes in

 

 15   immediate contact with the LDPE vial when it is use

 

 16   with self-adhesive paper labels.  This slide lists

 

 17   typical chemical composition of an adhesive.  This

 

 18   is not an all-inclusive list.  There are many more

 

 19   proprietary chemicals used in the formulation of

 

 20   these adhesives.  Depending upon the physical

 

 21   chemical properties of these chemicals, that is to

 

 22   say, volatility, they may permeate through the LDPE

 

                                                                43

 

  1   vial into the drug product.

 

  2             I have listed here some of the

 

  3   over-lacquer components.  Over-lacquer is an

 

  4   evaporative(?) coating which is typically comprised

 

  5   of chemicals such as plasticizers, resins,  (?)

 

  6   solvents, diluents, surfactants, and many more.

 

  7   Some of these chemicals are proprietary in nature.

 

  8   Over-lacquer, or varnish, may be used for a

 

  9   transparent glassy appearance of the label, also a

 

 10   stabilizer for the print work and art work, or it

 

 11   can be used as a protective barrier to the moisture

 

 12   and overall to extend the longevity of the label.

 

 13   Again, in this case also, depending upon the

 

 14   physical chemical properties of some of these

 

 15   chemicals and their constituents, also the

 

 16   concentration and storage conditions, these

 

 17   chemicals may have a potential to permeate through

 

 18   the LDPE vials into the drug product.

 

 19             These are typical ink components.  One may

 

 20   think that ink might be just a single-component

 

 21   formulation.  However, if you look at it, there is

 

 22   more than one chemical included into the ink

 

                                                                44

 

  1   formulation.  And, again, these are also propriety

 

  2   formulations.

 

  3             These ink formulations may be  (?)-based

 

  4   or organic solvent-based, and depending upon the

 

  5   brand of solvents which are used in the

 

  6   formulation, they may have a potential to permeate

 

  7   through the LDPE vials into the drug product.

 

  8             The last I would like to talk about is the

 

  9   foil-laminate.  Primarily, foil-laminate is used as

 

 10   a protective secondary packaging for the drug

 

 11   formulations that may be sensitive to light and

 

 12   react to gases such as oxygen.

 

 13             Typically, foil-laminate is a flexible

 

 14   packaging composed of multiple layers of various

 

 15   types of plastic films which are fused together

 

 16   either by heat or pressure-sensitive adhesives

 

 17   applied to one or both sides of an aluminum foil.

 

 18   In this cartoon, aluminum foil is represented by

 

 19   layer D, and as you can see, the whole foil

 

 20   overwrap surrounds the drug product vial on an

 

 21   automated packaging line.

 

 22             The thickness of aluminum foil, which is

 

                                                                45

 

  1   D, and the number of pinholes per unit area are

 

  2   crucial for ensuring the consistent barrier to

 

  3   permeability.  Furthermore, each of the composite

 

  4   layers may contain volatility chemicals, organic

 

  5   solvents, as they are used in adhesives, which may

 

  6   permeate through a LDPE vial into the drug product,

 

  7   especially the adhesive layer that is closer to the

 

  8   drug product.  In this case, that is shown by G.

 

  9   So the composition of these are very critical.  One

 

 10   has to really have a knowledge of its composition

 

 11   before they can be selected for the foil overwrap.

 

 12   Alternate approaches to adhesive can be considered,

 

 13   such as fusion of the multiple layers of

 

 14   foil-laminate by heat-set process.

 

 15             In addition to the clinical concerns

 

 16   discussed by Dr. Sullivan, the permeability of LDPE

 

 17   raises several quality concerns, and these are

 

 18   listed on this slide, mainly the drug product

 

 19   contamination through ingress of volatile chemicals

 

 20   which may be originating from the environment that

 

 21   may be irritant or toxic to the respiratory tract

 

 22   and may sensitize individuals; drug product

 

                                                                46

 

  1   degradation because of the reactive gases and light

 

  2   that permeate through the LDPE vial and cause

 

  3   degradation of the drug product; and change in

 

  4   product concentration because of the water

 

  5   evaporation through the LDPE vials.  This in turn

 

  6   can accelerate the drug product degradation because

 

  7   of the concentration of the drug product.

 

  8             Now, let me share with you the results of

 

  9   an analytical survey of approved NDA and ANDA

 

 10   inhalation solutions marketed in LDPE vials without

 

 11   protective overwrap.  The basis for this survey was

 

 12   a large-scale voluntary recall of inhalation

 

 13   solution by a firm due to contamination of the drug

 

 14   product with 1-phenoxypropanol.  This is a known

 

 15   component present in the packaging components.

 

 16   This recall was conducted with FDA's knowledge and

 

 17   followed by a health hazard evaluation.  It was

 

 18   later found out that the source of this chemical

 

 19   was the varnish or over-lacquer that was used for a

 

 20   shelf carton.

 

 21             Alarmed by this incident, the agency was

 

 22   concerned that there may be other inhalation drug

 

                                                                47

 

  1   products with such contamination from packaging

 

  2   components.  As a result, it was decided to conduct

 

  3   a product quality survey of some of the marketed

 

  4   inhalation solutions.

 

  5             This was initiated by the Office of

 

  6   Generic Drugs in consultation with the Division of

 

  7   Pulmonary and Allergy Drug Products and in

 

  8   coordination with the Office of Compliance, Office

 

  9   of Regulatory Affairs, field offices, and Pacific

 

 10   Regional Laboratory.  Seven ANDAs and one NDA for

 

 11   inhalation solutions covering five different drug

 

 12   substances were selected.

 

 13             There were 38 samples representing 37 lots

 

 14   of various drug products in LDPE vials without a

 

 15   protective overwrap foil pouch.  The samples were

 

 16   screened for potential volatile chemicals which are

 

 17   known to be present in the packaging components,

 

 18   such as vanillin, 2-phenoxyethanol, and

 

 19   1-phenoxy-2-propanol by sensitive analytical

 

 20   techniques such as GCMS and HPLC methods.  Let me

 

 21   share the results of this survey.

 

 22             Twenty-nine out of 38 samples tested

 

                                                                48

 

  1   positive for chemical contamination originating

 

  2   from packaging components.  Five known chemical

 

  3   contaminants, as listed below, were detected

 

  4   originating from packaging, such as benzophenone,

 

  5   polyethylene glycol, 2-(2-butoxyethoxy)ethanol,

 

  6   2-(2-ethoxyethoxy) ethanol acetate, and

 

  7   2-hydroxy-2-methylpropriophenone.

 

  8             A health hazard evaluation was conducted

 

  9   at the levels these components were detected in

 

 10   these drug products.  However, it was indicated

 

 11   that the levels of these components did not raise

 

 12   sufficient safety concern in the intended

 

 13   population to warrant a recall of these drug

 

 14   products.  Nonetheless, the following issues were

 

 15   of concern:

 

 16             It was indicated that potential for these

 

 17   chemicals to cause bronchospasm at levels detected

 

 18   is unknown, especially in patients with respiratory

 

 19   diseases.

 

 20             It was also indicated that concentration

 

 21   of these chemicals might be grater at the end of

 

 22   expiry than what was detected at the time they were

 

                                                                49

 

  1   tested.

 

  2             It also showed that permeation through

 

  3   LDPE vial is a real phenomenon.

 

  4             It was also concluded that additional

 

  5   chemicals may be present, but may not get detected

 

  6   because the analytical techniques which were used

 

  7   may not be suitable, not knowing what components

 

  8   might be present into those solutions.

 

  9             And, also, future changes in the materials

 

 10   used in labeling and packaging may result in

 

 11   contamination with different chemicals.

 

 12             So, in a nutshell, product contamination

 

 13   can occur because of the formulation component

 

 14   degradation or by leaching of chemical constituents

 

 15   from packaging components, such as resin components

 

 16   I have listed, paper label components, foil

 

 17   overwrap components, cartons, and environment.

 

 18             These are the typical extractable or

 

 19   leachable components which have been found in the

 

 20   drug product from packaging components.  Some of

 

 21   them are irganox 129, 2, 2, 6-trimethyloctane,

 

 22   which is coming from resin components.  Some of the

 

                                                                50

 

  1   paper label components that we have seen is benzoic

 

  2   acid, ethyl phthalate, benzophenone, danocur 1173,

 

  3   cyclic phthalates.  From the foil overwrap, we have

 

  4   seen methacrylic acid, 2-phenoxyethanol, and some

 

  5   of the organic solvents such as acetone,

 

  6   2-butanone, ethylacetate, propylacetate, heptane,

 

  7   and toluene.  And from cartons, methacrylic acid

 

  8   and 1-phenoxy-2-propanol.

 

  9             So this raises a significant quality

 

 10   concern, and there are several other factors.

 

 11   These are the factors.  Because of the proprietary

 

 12   nature of components and composition of this

 

 13   packaging material, we may not know what is present

 

 14   in the solution.  The composition of these

 

 15   components which are present in the packaging may

 

 16   change without the knowledge of applicant and the

 

 17   agency.  And you cannot detect if you don't know

 

 18   what you are looking for.  As a result, there is no

 

 19   one analytical procedure to detect unknown chemical

 

 20   contaminants.  And there is incomplete

 

 21   toxicological data or information available for

 

 22   many of these identified chemical contaminants. 

 

                                                                51

 

  1   And as the environmental conditions change, that

 

  2   may introduce new contaminants.

 

  3             So what are the potential approaches the

 

  4   agency has taken to minimize and control the

 

  5   contamination from packaging components to the

 

  6   extent possible?  Our approach has been and we have

 

  7   recommended that characterize or identify all

 

  8   possible extractables and establish a profile for

 

  9   each packaging component, for resin, vial, paper

 

 10   label, foil-laminate overwrap.

 

 11             What I mean by extractable is extractable

 

 12   is a chemical compound, which can be volatile or

 

 13   non-volatile, that gets extracted from a packaging

 

 14   component in a suitable solvent by utilizing

 

 15   optimum extraction conditions, such as time and

 

 16   temperature.

 

 17             Extractable profile for a given packaging

 

 18   component typically can be a chromatogram

 

 19   representing all possible extractables.

 

 20             After that, establish a correlation

 

 21   between extractable and its leachable potential,

 

 22   and what I mean by leachable is leachable is any

 

                                                                52

 

  1   chemical compound that leaches into the drug

 

  2   product formulation either from a packaging

 

  3   component or a local environment on storage through

 

  4   expiry of the drug product.  An extractable can be

 

  5   a leachable.

 

  6             And to ensure batch-to-batch consistency

 

  7   of the drug product, appropriate specification for

 

  8   a leachable is established based on its

 

  9   qualification and observed levels in the drug

 

 10   product on storage.

 

 11             As a result, the next approach is we asked

 

 12   them to set meaningful acceptance criteria for a

 

 13   given extractable in corresponding incoming

 

 14   packaging components based on its qualification

 

 15   level and actual observed data.  Once that is

 

 16   accomplished, meaningful acceptance criteria for a

 

 17   given leachable based on actual observed data in

 

 18   the drug product also be established.

 

 19             These are the recommendations we have

 

 20   provided in the Draft Guidance.  We have

 

 21   recommended that adequate knowledge of composition

 

 22   and physico-chemical properties of packaging

 

                                                                53

 

  1   components is essential for appropriate selection

 

  2   of these components.  We discourage paper label

 

  3   directly on the LDPE vial and encourage alternative

 

  4   approaches, including embossing or debossing, in

 

  5   lieu of the paper label on the LDPE vial because of

 

  6   the reasons I discussed, because of the product

 

  7   contamination.  This can be accomplished by

 

  8   extended bottom flanges to unit-dose vial that can

 

  9   carry essential vial labeling information and can

 

 10   retain the product identity.

 

 11             We have also recommended use of protective

 

 12   overwrap foil pouch for the LDPE unit-dose vial.

 

 13   This in turn can minimize the ingress and leaching

 

 14   of chemical contaminants from the local environment

 

 15   provided that the components that have been

 

 16   selected for the fabrication of the overwrap foil

 

 17   pouch are appropriately selected.

 

 18             The self-adhesive paper label on a foil

 

 19   pouch or pre-printed foil pouch is also

 

 20   recommended, and different color schemes to

 

 21   differentiate multiple strengths of the drug

 

 22   product is also recommended.  This in turn can

 

                                                                54

 

  1   prevent ingress or leaching of chemical

 

  2   contaminants from paper labels and may improve the

 

  3   legibility issues.

 

  4             The last recommendation we have in our

 

  5   Draft Guidance is to limit the number of unit-dose

 

  6   vials per pouch, ideally to one LDPE vial per foil

 

  7   pouch.  This can minimize the risk of medication

 

  8   error by patients and health care professionals,

 

  9   and it can prevent unnecessary exposure to local

 

 10   environment when compared to packaging of

 

 11   multi-unit-dose vials in a foil pouch.

 

 12             So, in summary, so far I have presented to

 

 13   you that volatile chemicals present in the

 

 14   packaging components and local environment have a

 

 15   great potential to permeate through LDPE vials into

 

 16   drug product formulation on storage.  The agency's

 

 17   analytical survey and other supportive data have

 

 18   confirmed ingress and leaching of such volatile

 

 19   chemicals into the drug product formulations.

 

 20             Ingress or leaching of such chemicals into

 

 21   drug product formulation poses a safety concern for

 

 22   patients with respiratory illnesses, such as asthma

 

                                                                55

 

  1   and COPD.  Embossing or debossing of LDPE vial in

 

  2   lieu of paper label is recognized to have

 

  3   legibility issue.  However, paper labels, although

 

  4   perceived to address legibility issue, overall may

 

  5   not be the optimum solution because of the safety

 

  6   concerns associated with potential leaching and

 

  7   ingress of paper label components in the drug

 

  8   product through LDPE vial.

 

  9             The agency's current recommendations as

 

 10   stated in the Draft Guidance may serve as a first

 

 11   step in the right direction to address the issues

 

 12   that are being discussed today.  And the agency is

 

 13   seeking other viable approaches to address these

 

 14   issues to promote safe product use without

 

 15   compromising the integrity of the drug product.

 

 16             With that, I will conclude my talk, and

 

 17   thank you for your attention.

 

 18             DR. GROSS:  Thank you very much, Dr. Shah,

 

 19   and I want to thank the first three speakers who

 

 20   presented a very clear review of the problem.

 

 21             We are now open for discussion.  Perhaps

 

 22   I'll start off with a couple questions.

 

                                                                56

 

  1             We talk about low-density polyethylene.

 

  2   Does high-density polyethylene reduce transmission,

 

  3   number one?  Number two, would increasing the

 

  4   thickness of the container reduce transmission?

 

  5   And, number three, have other plastics been

 

  6   considered?  I'm not a chemist so I don't know, but

 

  7   polypropylene, polystyrene?  And are any of those

 

  8   possibilities?

 

  9             DR. SHAH:  So far, traditionally, LDPE is

 

 10   the choice of material by the manufacturer because

 

 11   of some of the properties it can offer.  And I

 

 12   guess one can increase the thickness of the LDPE

 

 13   vial or may use a different polymer.  However, one

 

 14   has to keep in mind that by nature, when you do the

 

 15   fabrication of the vials, it may have some kind of

 

 16   a permeability.  But that depends on the degree of

 

 17   permeability.  LDPE offers one side of the

 

 18   spectrum, or other polymers may offer a different

 

 19   type of permeability.  But one has to conduct some

 

 20   of the studies to show that it does not permeate.

 

 21             DR. GROSS:  Michael?

 

 22             DR. COHEN:  Dr. Lee mentioned shrink wrap

 

                                                                57

 

  1   at one point, and then added that there might still

 

  2   be some concern about, you know, the volatility, I

 

  3   guess, of the inks in the shrink wrap itself.  It

 

  4   does not come in contact with the actual LDPE

 

  5   plastic, though, so I'm trying to figure out why

 

  6   that would be a concern.  Do you think it's still

 

  7   possible for that to leach in?

 

  8             DR. SHAH:  Yes, let me answer that.

 

  9   Shrink wrap, again, it's a plastic and it suffers

 

 10   through the same thing.  It comes in direct contact

 

 11   with the LDPE vial.  So depending upon the chemical

 

 12   components of the ink and how it is being used, in

 

 13   a shelf carton or anything, it still will have the

 

 14   same unit problems that I discussed.

 

 15             DR. COHEN:  Can I ask a follow-up?

 

 16             DR. GROSS:  Yes, go ahead, Michael.

 

 17             DR. COHEN:  Have you done testing--

 

 18             DR. SHAH:  No, we--I mean, we have not

 

 19   even received--or we have not approved a drug

 

 20   product with the shrink wrap.  There is no example

 

 21   of that, at least to CDER.  Maybe in other

 

 22   divisions, another agency, but we haven't received

 

                                                                58

 

  1   any.

 

  2             DR. GROSS:  Jackie, next question?

 

  3             DR. GARDNER:  I understand the problem of

 

  4   potentially masking the effect of contamination by

 

  5   the condition, but I was surprised to see only 87

 

  6   reports of medication errors that you're working

 

  7   from.  And given the excellent presentation and the

 

  8   potential for confusion, I'm surprised that there

 

  9   were so few because it looks like it would happen a

 

 10   lot.  I wondered if we could have some perspective

 

 11   on why there would be so few, and maybe Mike can

 

 12   help with that.

 

 13             And then the second thing is I wondered

 

 14   whether any of the potential suggested

 

 15   recommendations or the different packaging types

 

 16   have been tested in any way that we could

 

 17   reasonably expect that they might reduce the

 

 18   potential for error if they were implemented,

 

 19   whether the foil wrap or any of these things have

 

 20   been tested among the people who would be using

 

 21   them.

 

 22             DR. GROSS:  Next question, Leslie?

 

                                                                59

 

  1             Does anybody have an answer?  Marci?

 

  2             DR. LEE:  Thank you.  As to the number of

 

  3   reports being few, since the review was done, there

 

  4   have been additional reports submitted to the

 

  5   agency for a total, I think I said, of 138 reports,

 

  6   which may still sound like a small number, but

 

  7   considering the problem is probably very underreported.  We

 

  8   also had some reports that were

 

  9   describing errors that had to do with restocking.

 

 10   For example, a transport team's pouch was supposed

 

 11   to contain three Albuterol and three Ipatropium

 

 12   vials, and at this one given time it contained one

 

 13   vial of one drug and five of the other.  So, you

 

 14   know, in the report the narrative says, "We suspect

 

 15   that at least one patient has been affected by this

 

 16   problem."

 

 17             The same thing can happen in an inpatient

 

 18   setting where the drugs are getting intermixed in a

 

 19   bin.  So it's really an unknown, the actual impact

 

 20   of the problem.

 

 21             DR. GROSS:  Leslie?

 

 22             DR. HENDELES:  I'd like to just respond to

 

                                                                60

 

  1   Jackie's comment.  Mixing these medicines up is

 

  2   very unlikely to be associated with a visible toxic

 

  3   reaction, so that might be--if anything, the

 

  4   adverse consequences is a lack of therapeutic

 

  5   effect when you're treating a disease that's

 

  6   involving acute bronchospasm.  So the clinician

 

  7   can't distinguish between lack of drug effect from

 

  8   worsening of the disease.

 

  9             But the question I had was:  Is there any

 

 10   evidence that these contaminants in any way

 

 11   interact with the active drugs to either decrease

 

 12   their stability or to in some way inactivate them?

 

 13             DR. SHAH:  They may not inactivate, but

 

 14   they will increase the degradation of the products.

 

 15   They may react with the active, and then you will

 

 16   form an adduct.  But you are not going to, you

 

 17   know, inactivate the drug product.

 

 18             DR. SULLIVAN:  The other thing t keep in

 

 19   mind is that the list of potential contaminants is

 

 20   innumerable.  So what may be true of one chemical

 

 21   may not be true of the others.

 

 22             DR. GROSS:  Curt Furberg?

 

                                                                61

 

  1             DR. FURBERG:  I'd like to expand on that

 

  2   question.  What are the health effects of these