[Federal Register: December 26, 2006 (Volume 71, Number 247)]
[Proposed Rules]               
[Page 77314-77352]
From the Federal Register Online via GPO Access [wais.access.gpo.gov]
[DOCID:fr26de06-12]                         

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DEPARTMENT OF HEALTH AND HUMAN SERVICES

Food and Drug Administration

21 CFR Parts 201 and 343

[Docket No. 1977N-0094L]
RIN 0910-AF36

 
Internal Analgesic, Antipyretic, and Antirheumatic Drug Products 
for Over-the-Counter Human Use; Proposed Amendment of the Tentative 
Final Monograph; Required Warnings and Other Labeling

AGENCY: Food and Drug Administration, HHS.

ACTION: Proposed rule.

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SUMMARY: The Food and Drug Administration (FDA) is proposing to amend 
its over-the-counter (OTC) labeling regulations and the tentative final 
monograph (TFM) for OTC internal analgesic, antipyretic, and 
antirheumatic (IAAA) drug products to include new warnings and other 
labeling requirements advising consumers about potential risks and when 
to consult a doctor. FDA is also proposing to remove the alcohol 
warning in its regulations and add new warnings and other labeling for 
all OTC IAAA drug products. The new labeling would be required for all 
OTC drug products containing an IAAA active ingredient whether marketed 
under an OTC drug monograph or an approved new drug application (NDA). 
FDA is issuing this proposal as part of its ongoing review of OTC drug 
products after considering the advice of its Nonprescription Drugs 
Advisory Committee (NDAC) and other available information. FDA is 
proposing these labeling changes because it has tentatively concluded 
they are necessary for these ingredients to be considered generally 
recognized as safe and effective and not misbranded for OTC use. FDA 
will address information about the cardiovascular risks of nonsteroidal 
anti-inflammatory drugs (NSAIDs) that was discussed at a February 16-
18, 2005, FDA advisory committee meeting, and the ``Allergy alert'' 
warning for NSAID products, in a future issue of the Federal Register.

DATES: Submit written or electronic comments, including comments on 
FDA's economic impact determination, by May 25, 2007. The specified 
comment period is longer than is normally provided for proposed rules. 
Because of the complexity of the proposed rule, FDA is providing an 
additional 60 days (beyond the normal comment period) for comments to 
be submitted and does not plan to extend the comment period beyond this 
date. Please see section XV of this document for the proposed effective 
and compliance dates of any final rule that may publish based on this 
proposal.

ADDRESSES: You may submit comments, identified by Docket No. 1977N-
0094L and Regulatory Information Number (RIN) 0910-AF36 by any of the 
following methods:
Electronic Submissions
    Submit electronic comments in the following ways:
     Federal eRulemaking Portal: http://frwebgate.access.gpo.gov/cgi-bin/leaving.cgi?from=leavingFR.html&log=linklog&to=http://www.regulations.gov. 

Follow the instructions for submitting comments.
     Agency Web site: http://frwebgate.access.gpo.gov/cgi-bin/leaving.cgi?from=leavingFR.html&log=linklog&to=http://www.fda.gov/dockets/ecomments. 

Follow instructions for submitting comments on the agency Web site.
Written Submissions
    Submit written submissions in the following ways:
     FAX: 301-827-6870.
     Mail/Hand delivery/Courier [For paper, disk, or CD-ROM 
submissions]: Division of Dockets Management (HFA-305), Food and Drug 
Administration, 5630 Fishers Lane, rm. 1061, Rockville, MD 20852.
    To ensure more timely processing of comments, FDA is no longer 
accepting comments submitted to the agency by e-mail. FDA encourages 
you to continue to submit electronic comments by using the Federal 
eRulemaking Portal or the agency Web site, as described in the 
Electronic Submissions portion of this paragraph.
    Instructions: All submissions received must include the agency name 
and Docket No. and RIN for this rulemaking. All comments received may 
be posted without change to http://frwebgate.access.gpo.gov/cgi-bin/leaving.cgi?from=leavingFR.html&log=linklog&to=http://www.fda.gov/ohrms/dockets/default.htm
, including any personal information provided. For 

additional information on submitting comments, see the ``Comments'' 
heading of the SUPPLEMENTARY INFORMATION section of this document.
    Docket: For access to the docket to read background documents or 
comments received, go to http://frwebgate.access.gpo.gov/cgi-bin/leaving.cgi?from=leavingFR.html&log=linklog&to=http://www.fda.gov/ohrms/dockets/default.htm 

and insert the docket number(s), found in brackets in the heading of 
this document, into the ``Search'' box and follow the prompts and/or go 
to the Division of Dockets Management, 5630 Fishers Lane, rm. 1061, 
Rockville, MD 20852.

FOR FURTHER INFORMATION CONTACT: Marina Chang, Center for Drug 
Evaluation and Research, Food and Drug Administration, 10903 New 
Hampshire Ave., Silver Spring, MD, 20993-0002, 301-796-2090.

[[Page 77315]]


SUPPLEMENTARY INFORMATION:

Table of Contents

I. Introduction
II. Background
    A. Development of OTC IAAA Drug Product Warnings
    B. Completion of the OTC IAAA Drug Products Final Monograph (FM)
III. NDAC Meeting
    A. Data and Information Reviewed
    B. Acetaminophen
    C. Aspirin and Other NSAIDs
IV. Additional Data and Information FDA Reviewed
    A. Pre-existing Liver Disease as a Risk Factor for Acetaminophen 
Hepatotoxicity
    B. Updated Literature about Acetaminophen Toxicity
    C. Aspirin and Other NSAIDs
V. FDA's Tentative Conclusions
    A. Acetaminophen
    B. Aspirin and Other NSAIDs
VI. FDA's Proposal
    A. Alcohol Warning
    B. Acetaminophen
    C. Aspirin and other NSAIDs
    D. Requirements to Supplement Approved Applications
    E. Regulatory Action
    F. Conforming Changes to the OTC IAAA TFM
VII. Additional Issues for Consideration
    A. Safe and Effective Daily Acetaminophen Dose
    B. Daily Dose Recommendations for Alcohol Abusers
    C. Combinations With Methionine or Acetylcysteine
    D. Package Size and Configuration Limitations
    E. Label Warning for Individuals With Human Immunodeficiency Virus 
(HIV)
    F. Drug Interactions Between Acetaminophen and Warfarin
VIII. Legal Authority
    A. Statement About Warnings
    B. Marketing Conditions
IX. Voluntary Implementation
X. Analysis of Impacts
    A. Need for the Rule
    B. Impact of the Rule
    C. Impact on Affected Sectors
    D. Alternatives
    E. Benefits
XI. Paperwork Reduction Act of 1995
XII. Environmental Impact
XIII. Federalism
XIV. Request for Comments
XV. Proposed Effective and Compliance Dates
XVI. References

I. Introduction

    FDA is proposing to: (1) Amend the TFM for OTC IAAA drug products, 
(2) remove the alcohol warning, and (3) add new warnings and other 
labeling for all OTC IAAA drug products. The proposed warnings and 
other labeling requirements will advise consumers of potential risks 
and when to consult a doctor. More specifically, FDA is proposing the 
following changes to the labeling:
     Requiring a new liver warning for products that contain 
acetaminophen.
     Requiring a new stomach bleeding warning for products that 
contain an NSAID (e.g., aspirin or ibuprofen).
     Removing the alcohol warning currently required for all 
OTC IAAA drug products in Sec.  201.322 (21 CFR 201.322) and 
incorporating an alcohol warning in the new liver warning for 
acetaminophen and the new stomach bleeding warning for NSAIDs.
     Requiring that the ingredient acetaminophen be prominently 
identified on the product's principal display panel (PDP) of the 
immediate container and the outer carton, if applicable.
     Requiring that the name of the NSAID ingredient followed 
by the term ``NSAID'' be prominently identified on the product's PDP of 
the immediate container and the outer carton, if applicable.
    This new labeling would be required for all OTC drug products 
containing an IAAA active ingredient, whether marketed under an OTC 
drug monograph or an approved NDA. FDA bases this proposal on its 
reviews of the medical literature, data provided to FDA, and 
recommendations made by NDAC. FDA has tentatively concluded that new 
labeling for OTC IAAA drug products is necessary for the safe and 
effective use of these products by consumers.

II. Background

    FDA believes that acetaminophen and NSAIDs, when labeled 
appropriately and used as directed, are safe and effective OTC drug 
products that benefit tens of millions of consumers every year. FDA 
believes that these products should continue to be accessible to 
consumers in the OTC setting.
     Internal analgesics have long been very effective OTC drug 
products for the intermittent treatment of minor aches and pains and 
fever.
     At their recommended OTC doses, these products are only 
rarely associated with serious adverse events relative to the number of 
consumers who use these products.

A. Development of OTC IAAA Drug Product Warnings

    The development of a monograph for OTC IAAA drug products began in 
1977 with publication of an expert panel report and continued in 1988 
with publication of the TFM. The development of labeling for OTC IAAA 
drug products is recorded in the following documents.
1. Warnings for Aspirin and Acetaminophen
    In the Federal Register of July 8, 1977 (42 FR 35346), FDA 
published the report of the Advisory Review Panel on OTC Internal 
Analgesic, Antipyretic, and Antirheumatic Drug Products (the IAAA 
Panel) for OTC IAAA active ingredients: Acetaminophen, aspirin, 
carbaspirin calcium, choline salicylate, magnesium salicylate, and 
sodium salicylate. The recommendations included labeling and warnings 
for:
     Aspirin: ``Caution: Do not take this product if you have 
stomach distress, ulcers or bleeding problems except under the advice 
and supervision of a physician'' (42 FR 35346 at 35387), and
     Acetaminophen: ``Do not exceed recommended dosage because 
severe liver damage may occur'' (42 FR 35346 at 35415).
    In the Federal Register of November 16, 1988 (53 FR 46204), FDA 
published a tentative monograph with the following warnings for:
     Aspirin: ``Do not take this product if you have stomach 
problems (such as heartburn, upset stomach, or stomach pain) that 
persist or recur, or if you have ulcers or bleeding problems, unless 
directed by a doctor'' (53 FR 46204 at 46256), and
     Acetaminophen: ``Prompt medical attention is critical for 
adults as well as for children even if you do not notice any signs or 
symptoms.'' This warning follows the general overdose warnings in 21 
CFR 330.1(g) (53 FR 46204 at 46213).
2. Warnings in the Professional Labeling for Aspirin
    In the Federal Register of October 23, 1998 (63 FR 56802), FDA 
published labeling for health professionals (not available in OTC drug 
product labeling) that provided for cardiovascular and rheumatologic 
indications. The labeling listed adverse reactions reported in the 
literature, e.g., hypotension (low blood pressure); tachycardia (rapid 
heart rate); dizziness; headache; dyspepsia (indigestion); bleeding, 
ulceration, and perforation of the gastrointestinal (GI) tract; nausea; 
and vomiting. FDA determined that consumers were not able to determine 
when they needed to take aspirin to prevent cardiovascular events, such 
as stroke, myocardial infarction (damage to the heart muscle), or other 
conditions. FDA did not

[[Page 77316]]

consider it possible to provide adequate directions and warnings to 
enable the layperson to make a reasonable self-diagnosis of these 
cardiovascular and rheumatologic conditions.
3. Alcohol Warnings for Acetaminophen and NSAIDs
    In the Federal Register of October 23, 1998 (63 FR 56789), FDA 
published a final regulation stating that any OTC drug product, labeled 
for adult use, containing acetaminophen, aspirin, carbaspirin calcium, 
choline salicylate, ibuprofen, ketoprofen, magnesium salicylate, 
naproxen sodium, and sodium salicylate must bear an alcohol warning 
statement in its labeling. Section 201.322 requires the following 
statements:
     For products containing acetaminophen:
    Alcohol Warning: If you consume 3 or more alcoholic drinks every 
day, ask your doctor whether you should take acetaminophen or other 
pain relievers/fever reducers. Acetaminophen may cause liver damage.
     For products containing aspirin, carbaspirin calcium, 
choline salicylate, ibuprofen, ketoprofen, magnesium salicylate, 
naproxen sodium, and sodium salicylate:
    Alcohol Warning: If you consume 3 or more alcoholic drinks every 
day, ask your doctor whether you should take (name of active 
ingredient) or other pain relievers/fever reducers. (Name of active 
ingredient) may cause stomach bleeding.
     For products containing acetaminophen with other IAAA 
active ingredients:
    Alcohol Warning: If you consume 3 or more alcoholic drinks every 
day, ask your doctor whether you should take (insert acetaminophen and 
one other IAAA active ingredient--including, but not limited to 
aspirin, carbaspirin calcium, choline salicylate, magnesium salicylate, 
or sodium salicylate) or other pain relievers/fever reducers. 
Acetaminophen and (insert name of one other IAAA active ingredient--
including, but not limited to aspirin, carbaspirin calcium, choline 
salicylate, magnesium salicylate, or sodium salicylate) may cause liver 
damage and stomach bleeding.
4. Proposed Amendment to Include Ibuprofen as a Generally Recognized 
Safe and Effective OTC IAAA Active Ingredient
    In the Federal Register of August 21, 2002 (67 FR 54139), FDA 
proposed to include ibuprofen in the monograph for OTC IAAA drug 
products with additional warnings:
    Ask a doctor before use if you have:
     Problems or serious side effects from taking pain 
relievers or fever reducers
     Stomach problems that last or come back, such as 
heartburn, upset stomach, or pain
     Ulcers
     Bleeding problems
     High blood pressure, heart or kidney disease, are taking a 
diuretic, or are over 65 years of age.
    FDA received several comments (Refs. 1 and 2) about the proposed 
warning for kidney disease and reopened the administrative record on 
June 4, 2003 (68 FR 33429), to allow for additional public comment. FDA 
continues to propose a warning about kidney disease for ibuprofen and 
other NSAIDs in this document. In a future issue of the Federal 
Register, we will publish our final decision about this warning and the 
proposed inclusion of ibuprofen in the monograph.

B. Completion of the OTC IAAA Drug Products FM

    In the process of completing the FM for OTC IAAA drug products, FDA 
reviewed a variety of data regarding the safety of acetaminophen, 
aspirin, and other NSAIDs. FDA continued to receive serious adverse 
event reports associated with the use of these products during this 
review. These serious adverse events included unintentional 
acetaminophen hepatotoxicity and NSAID-related GI bleeding and renal 
toxicity. Although the occurrence of these events is rare, relative to 
the extensive use of the products, as described in the text that 
follows, FDA believes that labeling changes are necessary for the safe 
and effective use of these products and to reduce the associated 
morbidity.
1. Unintentional Acetaminophen Hepatotoxicity
    Acetaminophen is widely available in numerous single ingredient and 
combination OTC drug products, and in many prescription drug products, 
as a pain reliever and/or fever reducer. OTC acetaminophen drug 
products, as currently labeled and used, have been reported to be 
associated with unintentional overdose that may lead to serious 
hepatotoxicity (Ref. 3). The IAAA Panel discussed overdose-related 
hepatotoxicity (42 FR 35346 at 35413 to 35414), and FDA addressed it in 
the IAAA TFM (53 FR 46204 at 46213 to 46218). (See section II.A.1 of 
this document.)
2. Aspirin and Other NSAIDs--GI Bleeding and Renal Toxicity
    Aspirin and other NSAIDs are available OTC for the treatment of 
minor aches and pain, for the treatment of headaches, and for fever 
reduction. Per aspirin's professional labeling (not part of the OTC 
drug product labeling), aspirin may be used to reduce the risk of 
serious cardiovascular events when taken on a daily basis under the 
direction of a physician. Aspirin is also effective in treating a 
variety of rheumatologic diseases under the direction of a physician. 
The professional labeling also includes information about the potential 
risk of GI bleeding and renal toxicity associated with aspirin.
    OTC nonaspirin salicylates include the NSAIDs ibuprofen, naproxen 
sodium, and ketoprofen. The product labels for these products are not 
required to contain warnings about GI bleeding and renal toxicity. 
These ingredients are, however, also available by prescription at 
strengths higher than in OTC products and the prescription product 
labeling contains warnings about these risks.

III. NDAC Meeting

    At a September 19 and 20, 2002, meeting, NDAC considered products 
currently marketed with OTC IAAA ingredients, including acetaminophen, 
aspirin, carbaspirin calcium, choline salicylate, ibuprofen, 
ketoprofen, magnesium salicylate, naproxen sodium, and sodium 
salicylate. FDA expressed its belief that these products should remain 
available OTC given their overall effectiveness and safety, the benefit 
to consumers of having a pain reliever and fever reducer available OTC, 
and the use of these products by tens of millions of people weekly. FDA 
suggested that certain interventions could decrease the frequency and 
morbidity of these serious adverse events. NDAC members were asked to 
consider which additional interventions were necessary to reduce the 
occurrence of serious adverse events. The presentations made at the 
meeting, and NDAC's findings, are summarized in this document. More 
information about the September 2002 NDAC meeting is available on the 
Internet and in the Division of Dockets Management (see ADDRESSES).

A. Data and Information Reviewed

    FDA provided NDAC with the following data and information (Ref. 3):
     Applicable sections of rulemakings for OTC IAAA active 
ingredients.

[[Page 77317]]

     Proposed and final rules for the alcohol warning for OTC 
IAAA drug products.
     Final rule for professional labeling of OTC drug products 
containing aspirin.
     Amendment to propose inclusion of ibuprofen in the 
monograph for OTC IAAA drug products.
     For acetaminophen, FDA reviews of data, poisoning data in 
Toxic Exposure Surveillance System (TESS), exposure data from poison 
control centers, overdose reference articles, and an abstract 
describing trends in acute liver failure in the United States.
     For aspirin/NSAIDs, FDA reviews of data and articles from 
the medical literature.
    NDAC also considered submissions and presentations from industry 
and individuals during the open public sessions (Refs. 4 and 5).

B. Acetaminophen

    On the first day of the meeting (September 19, 2002), NDAC 
considered safety issues related to the use of acetaminophen, 
unintentional overdose, and the potential for hepatotoxicity from both 
OTC and prescription acetaminophen products.
1. Points for Discussion
    FDA asked NDAC to discuss possible factors that might contribute to 
unintentional overdose (Ref. 3) and provided the following points for 
consideration:
     Acetaminophen is available to consumers in many OTC and 
prescription drug products (i.e., single ingredient and combinations 
with various other active ingredients).
     Consumers fail to identify acetaminophen as an ingredient 
in their OTC and prescription drug products.
     Consumers are unaware of the risks of exceeding the 
recommended dose of acetaminophen with a single product, or of 
simultaneously using multiple products containing acetaminophen.
    FDA asked NDAC what additional measures could be taken to better 
ensure that prescribers and other people are aware of the potential 
risks associated with exceeding the recommended dose of prescription or 
OTC drug products containing acetaminophen and with using multiple 
products containing acetaminophen. FDA suggested the following possible 
measures for OTC drug products:
     Consumer education
     Changes in labeling that identify and highlight the risks
     Packaging that may enhance appropriate use
     Consumer inserts.
    For prescription products, FDA suggested:
     Unit of use packaging with labeling on each blister pack
     Physician and pharmacist education
     Publication of information in professional journals
     Consumer education
     FDA publications to identify and highlight the danger and 
risk
     Providing patient information leaflets and stickers when 
dispensing the prescription.
    FDA also asked NDAC if there are identifiable factors that might 
make some individuals more susceptible to hepatic toxicity (e.g., 
underlying liver disease, malnutrition, drug interactions, and alcohol 
users). If subpopulations at increased risk of acetaminophen-induced 
hepatotoxicity could be identified, FDA asked NDAC what reasonable 
measures could be taken to decrease their risk. FDA suggested some 
possible measures:
     Adjustment of the maximum total daily dose or dosing 
interval
     Changes in labeling that identify the population and 
highlight the risks
     Additional research on specific subpopulations
     Consumer and physician education.
    FDA asked NDAC whether additional studies are needed to evaluate 
these issues. FDA suggested a number of subjects for potential 
research:
     Evaluation of the effectiveness of educational programs
     Evaluation of revised labeling
     Surveillance of serious acetaminophen hepatotoxicity cases
     Enhanced collection of information when medication errors 
occur
     Better understanding of consumer use of these products.
2. Presentations and Submissions to NDAC
    As a lead-in to the liver toxicity discussion, Dr. William Lee, of 
the University of Texas Southwestern Medical Center at Dallas, 
presented the results of acute liver failure (ALF) studies in the 
United States (Ref. 6). He estimated that between 1,000 and 2,000 ALF 
cases occur in the United States each year and are associated with high 
mortality. Dr. Lee conducted a retrospective analysis of 177 cases of 
ALF reported in the literature between 1986 and 1998. Of these, 20 
percent were attributed to acetaminophen toxicity. To study ALF 
prospectively, Dr. Lee also formed a study group of 25 treatment 
centers in 1998. Details of the group's initial 308 cases are presented 
in table 1. Approximately 40 percent of the cases were due to 
acetaminophen toxicity, which was increased when compared to the rate 
of acetaminophen toxicity in the cohort from Dr. Lee's retrospective 
analysis.

                                                  Table 1.-- Study Group Series of ALF Cases (N = 308)
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                                                                                                  ALF Etiology
                                                       -------------------------------------------------------------------------------------------------
                   Case Report Data                                                                                               All Other
                                                          Acetaminophen Induced    Drug (Not Acetaminphen)     Indeterminate       Causes       P value
                                                                 (n=120)               Induced (n=40)          Cause (n=53)        (n=95)
--------------------------------------------------------------------------------------------------------------------------------------------------------
Sex (% Female)                                                              79                        73                  60            72       NS*
--------------------------------------------------------------------------------------------------------------------------------------------------------
Age (years)                                                                 36                        41                  38            43         0.02
--------------------------------------------------------------------------------------------------------------------------------------------------------
Jaundice (days)                                                              1                        12                  12             4        < 0.001
--------------------------------------------------------------------------------------------------------------------------------------------------------
Coma (%)                                                                    50                        43                  47            47        NS
--------------------------------------------------------------------------------------------------------------------------------------------------------
Alanine aminotransferase (ALT) (International Units/                      4310                       574                 947          1060        < 0.001
 Liter (IU/L))**
--------------------------------------------------------------------------------------------------------------------------------------------------------
Bilirubin                                                                    4.3                      20.2                24.5          12.6      < 0.001
--------------------------------------------------------------------------------------------------------------------------------------------------------

[[Page 77318]]


Transplant (%)                                                               6                        53                  51            36        < 0.001
--------------------------------------------------------------------------------------------------------------------------------------------------------
Spontaneous survival (%)                                                    68                        25                  17            33        < 0.001
--------------------------------------------------------------------------------------------------------------------------------------------------------
Overall survival (%)                                                        73                        70                  64            61        NS
--------------------------------------------------------------------------------------------------------------------------------------------------------
* Not significant ** ALT (normal range 0-35 IU/L)

    Of the 120 acetaminophen toxicity cases identified in Dr. Lee's 
series, 12 were omitted due to concomitant patient issues that would 
have confounded the analysis. The remaining 108 cases were analyzed and 
showed that alcohol use was reported in 57 percent of the cases and 
alcohol abuse was reported in 19 percent of the cases. Individuals in 
38 percent of the cases were taking both narcotic-acetaminophen 
prescription products and OTC acetaminophen products at the same time, 
some for as long as 2 to 3 months. In 70 percent of the cases, patients 
ingested more than 4 grams (g) of acetaminophen per day (recommended 
maximum daily dose), and 32 percent of the cases reported ingestion of 
more than 10 g per day.
    A comparison was conducted among the 108 cases of toxicity due to 
accidental (ingestion of drugs for pain relief, without suicidal 
intent) and suicidal (ingestion with admitted suicidal attempt) 
ingestion. The type of ingestion could not be determined in 5 cases, 
resulting in a comparison of 103 cases (table 2). More than half of the 
acetaminophen toxicity cases (57 percent) were accidental.

                            Table 2.--Suicidal vs. Accidental Acetaminophen ALF Cases
----------------------------------------------------------------------------------------------------------------
                                         Accidental (n=59)          Suicidal (n=44)              p-value
----------------------------------------------------------------------------------------------------------------
Age                                                      39                        33                     0.011
----------------------------------------------------------------------------------------------------------------
Acetaminophen total (g)                                  20                        29                    NS
----------------------------------------------------------------------------------------------------------------
Antidepressant                                          36%                       34%                    NS
----------------------------------------------------------------------------------------------------------------
Alcohol (non-abuse use)                                 55%                       61%                    NS
----------------------------------------------------------------------------------------------------------------
Double use*                                             24%                        5%                     0.02
----------------------------------------------------------------------------------------------------------------
Narcotic/acetaminophen                                  54%                       14%                     0.001
----------------------------------------------------------------------------------------------------------------
ALT (IU/L)                                            3,616                     5,929                    < 0.001
----------------------------------------------------------------------------------------------------------------
Creatine                                                  2.5                       1.3                   0.008
----------------------------------------------------------------------------------------------------------------
Survival                                                71%                       75%                    NS
----------------------------------------------------------------------------------------------------------------
* Use of more than one acetaminophen containing product.

    The incidence of use of antidepressants and alcohol was nearly 
identical in the accidental and suicidal groups. The accidental cases 
included a larger percentage of subjects who double-dosed or used a 
narcotic/acetaminophen combination product. Survival rates were also 
similar. Lee concluded that acetaminophen toxicity accounted for about 
a third of all deaths from ALF in this case series and appears to be a 
growing problem in the United States.
    FDA staff presented a safety analysis of hepatotoxicity associated 
with acetaminophen (Ref. 7). The cases were reported as ``intentional 
overdose'' and ``unintentional overdose.'' The reported doses were 
rarely within the recommended range. Four national databases were used 
to estimate the occurrence of these events:
    1. National Hospital Ambulatory Care Survey: Emergency Department 
(ED) Component--a probability survey sampling of visits made to 
emergency departments and short stay hospitals in the United States.
    2. National Electronic Injury Surveillance System--collects 
information on consumer product-related injuries treated in emergency 
departments of 66 selected hospitals.
    3. National Hospital Discharge Survey--a probability survey 
sampling of patient discharge records from non-Federal, short stay 
hospitals in the United States.
    4. Multiple Cause of Death Files--a data file that contains 
information from death certificates.
    Acetaminophen overdose (unintentional and intentional) was 
associated with an annual average of over 56,000 emergency department 
visits (1993 to 1999) and more than 26,000 hospitalizations (1990 to 
1999). Between 1996 and 1998, an annual average of 458 deaths was 
attributed, at least in part, to acetaminophen overdose. Unintentional 
acetaminophen overdose was associated with an annual average of over 
13,000 emergency department visits (1993 to 1999), 2,189 
hospitalizations (1990 to 1999), and 100 deaths (1996 to 1998). Each 
event in these tallies is independent from the others. No information 
about associated

[[Page 77319]]

hepatotoxicity was available for these cases. FDA reviewed the age 
distribution for acetaminophen overdoses. Medication use varies by age 
and different OTC drug products containing acetaminophen are available 
for different age groups. The age distribution of unintentional 
overdose cases varies among reporting databases and is shown in table 
3. While emergency department visits are most prevalent among young 
people, this age group accounts for the lowest percentage of cases of 
mortality.

                                Table 3.--Age Distribution of Unintentional Cases
----------------------------------------------------------------------------------------------------------------
                                                                   Age (years)
                                --------------------------------------------------------------------------------
                                            <17                       17--64                      >65
----------------------------------------------------------------------------------------------------------------
Emergency department visit                             74%                        25%                        < 1%
----------------------------------------------------------------------------------------------------------------
Hospitalization                                        23%                        70%                         7%
----------------------------------------------------------------------------------------------------------------
Mortality                                               1%                        75%                        23%
----------------------------------------------------------------------------------------------------------------

    Chronic liver disease has been postulated to be one of the factors 
that increases the risk of hepatotoxicity from acetaminophen. Using the 
multiple cause of death database, the presence of chronic liver disease 
among cases of unintentional and intentional overdose with mortality 
outcomes was examined (table 4).

 Table 4.--Percent of Liver Disease Reported Among Fatal Acetaminophen Overdose Cases, Mortality Data, 1996-1998
----------------------------------------------------------------------------------------------------------------
               Liver Disease Reported                     Unintentional (N=235)         Intentional (N=1,010)
----------------------------------------------------------------------------------------------------------------
Chronic alcoholic                                                              13%                            1%
----------------------------------------------------------------------------------------------------------------
Other chronic liver disease                                                    48%                            8%
----------------------------------------------------------------------------------------------------------------

    These findings suggest that chronic liver disease, in the presence 
or absence of alcohol, may be a risk factor for developing or 
increasing severity of hepatotoxicity among people with unintentional 
overdose. However, this analysis has limitations. If the presence of 
alcohol or alcohol use was not mentioned on the death certificate, 
alcohol related liver disease may be misclassified as other chronic 
liver disease. In addition, suicide cases may be misclassified as 
unintentional overdose to protect privacy.
    FDA also presented an analysis of cases of hepatotoxicity 
associated with acetaminophen from the published literature. A MEDLINE 
search identified all U.S. case series containing at least 10 cases 
that had been published in the previous 10 years (Ref. 7). Eight case 
series were identified, four of which were derived exclusively from 
review of hospital medical charts. In two series, cases were obtained 
from hospitals, published cases, the FDA adverse event reporting 
system, and poison control center databases. One case series was from a 
registry of cases reported by hepatologists and other practitioners. 
One case series was obtained exclusively from a consortium of liver 
transplant centers. The number of cases per series ranged from 47 to 
73. Two case series were largely pediatric, and the remaining six case 
series consisted of largely adult populations. Six of the case series 
reported gender, and in all six there was a preponderance of females. 
Intentionality was reported in five of the series. Table 5 shows the 
acetaminophen dose reported among in the unintentional overdose groups.

                          Table 5.--Hepatotoxicity Series: Unintentional Toxicity Cases
----------------------------------------------------------------------------------------------------------------
                                                                                      No. of Cases With Typical
      Case Series       Reported Daily Doses (g/day)     No. of Cases in Series        Daily Dose of < =4g/day
----------------------------------------------------------------------------------------------------------------
Johnston                                      1.3-20                            53                             9
----------------------------------------------------------------------------------------------------------------
Schiodt                                         2-30                            21                             3
----------------------------------------------------------------------------------------------------------------
Zimmerman                            ``<4''-``>15''*                            67                            27
----------------------------------------------------------------------------------------------------------------
Whitcomb                                      3.5-25                            21                          None
----------------------------------------------------------------------------------------------------------------
Broughan                                 15.9 (mean)                             8                          None
----------------------------------------------------------------------------------------------------------------
* Dose was reported categorically.

    Nine people in the Johnston case series and three people in the 
Schiodt case series ingested 4 g/day or less of acetaminophen. In the 
Zimmerman case series, 27 people used acetaminophen at the recommended 
dose, while 13 people used between 4.1 and 6 g/day. In the Whitcomb 
case series, 3 people used acetaminophen at, or slightly above, the 
recommended dose (i.e., 3.5 to 5 g/day in one case and 4 to 6 g/day in 
two cases). In the Broughan case study, none of the people took 
acetaminophen at the recommended dose.

[[Page 77320]]

    Table 6 compares the number of deaths and serious outcomes for the 
unintentional and intentional groups. Intentionality could only be 
compared in the adult case series. Serious outcomes were defined as 
hepatic coma, acute liver failure, and liver transplant.

    Table 6.--Comparison of Unintentional and Intentional Toxicity Groups: Cases of Death or Serious Outcome
----------------------------------------------------------------------------------------------------------------
                     Case Series                              Unintentional                  Intentional
----------------------------------------------------------------------------------------------------------------
Johnston                                                                     17/53                           NA*
----------------------------------------------------------------------------------------------------------------
Schiodt                                                                      11/21                          4/50
----------------------------------------------------------------------------------------------------------------
Zimmerman                                                                    13/67                           NA*
----------------------------------------------------------------------------------------------------------------
Whitcomb                                                                      5/21                          NR**
----------------------------------------------------------------------------------------------------------------
Broughan                                                                       2/8                          0/40
----------------------------------------------------------------------------------------------------------------
*NA: Not applicable; **NR: Not reported

    FDA also presented case data from the TESS of the American 
Association of Poison Control Centers (AAPCC). At that time, AAPCC had 
a repository of over 27 million human poison exposures reported by over 
60 participating centers. These centers covered over 90 percent of the 
U.S. population. Examination of AAPCC's annual reports from 1995 to 
1999 of cases listing acetaminophen as the primary (first) agent showed 
acetaminophen to be the leading cause of poisonings. In 1999, 
acetaminophen-related calls represented 10 percent of all calls to 
AAPCC. There was a decrease in calls between 1995 (111,175) and 1999 
(108,102). In 1999, nearly 50 percent of the poison victims associated 
with the calls received treatment in health care facilities. Two 
percent of these victims were reported to have developed major effects 
resulting from the poisoning, i.e., the signs or symptoms occurring as 
a result of acetaminophen exposure were life-threatening or resulted in 
significant residual disability. Fifty percent of the calls involved 
children and adolescents (19 years of age or under). Of the 
acetaminophen related calls regarding children under 6 years of age 
(approximately 40,000 calls), 22 percent occurred in children who 
ingested adult formulations of acetaminophen.
    In 1995, there were at least 76 acetaminophen-related fatalities. 
By 1999, the number of acetaminophen-related fatalities increased to 
141. Of these, 92 (65 percent) were a result of suicidal intent, 43 (30 
percent) were unintentional, and the dosing intent for 6 (4 percent) 
was undetermined. Among the 43 unintentional fatalities, 28 (65 
percent) took one OTC drug product containing only acetaminophen; 4 (9 
percent) took one prescription product containing acetaminophen, and 11 
(26 percent) took more than one acetaminophen product simultaneously. 
These AAPCC data may underreport the actual number of acetaminophen 
toxicity cases, because serious cases that go directly to emergency 
departments, and chronic users of acetaminophen, are unlikely to 
generate poison control center contacts.
    FDA staff reviewed spontaneous reports of hepatoxicity in FDA's 
adverse event reporting system (AERS). U.S. cases were identified that 
had been received by FDA between January 1998 and July 2001 and in 
which one or more acetaminophen containing products had been ingested. 
Of 633 reports, 43 were duplicates. Another 283 were excluded for 
various reasons, primarily to exclude cases in which there was apparent 
suicidal intent. A total of 307 cases were included in FDA's analysis 
(25 pediatric and 282 adult cases).
    Pediatric cases (of children age 1 day to 8 years) consisted 
primarily of males (approximately 70 percent), although gender was not 
reported in each case. Fifteen of the 25 pediatric cases involved 
severe, life-threatening liver injury. Of the 25 children, 10 died, 21 
were hospitalized, and 2 required only treatment in an emergency 
department. The dose was estimated, based upon reported daily doses and 
weight, in 10 cases to be 106 to 375 milligrams/kilogram (mg/kg) per 
day. The recommended pediatric dose is 75 mg/kg/day (Ref. 7). Twenty-
two of the children (88 percent) took only 1 product containing 
acetaminophen and 3 children (12 percent) took 2 or more products 
containing acetaminophen. Sixteen of the cases (53 percent) reported 
ingestion of a single ingredient acetaminophen product (APAP), 12 cases 
(40 percent) reported ingestion of an ``unspecified APAP product'' and 
the remainder of the cases reported ingestion of combination products. 
Of the single ingredient products, concentrated drops containing 
acetaminophen 100 mg/milliliter (mL) were reportedly ingested in seven 
cases.
    In 20 of the pediatric cases, 1 or more medication errors were 
reported. In three cases, the wrong product was used, i.e., the 
concentrated drops instead of the children's acetaminophen liquid 
formulation. In four cases, incorrect measuring devices were used, 
i.e., teaspoonfuls instead of dropperfuls. Five cases reported 
instances of misinterpretation of labeled dosing guidelines or 
misinterpretation of instructions provided by a health care provider.
    Sixty percent of the 282 adult cases (15 to 85 years old) were 
female and 229 required hospitalization. A total of 169 adults 
experienced severe, life-threatening liver injury; 124 of these 
patients died and 7 required a liver transplant. One hundred ninety-
nine (71 percent) adults reported using an acetaminophen product for a 
therapeutic indication, primarily analgesia. In 74 (26 percent) cases, 
the indication for use was unknown, and in 9 (3 percent) cases, abuse 
of a narcotic-acetaminophen prescription product was reported. One 
hundred thirty-eight (38 percent) cases listed an unspecified 
acetaminophen product (unknown whether single ingredient or combination 
product and whether OTC or prescription), 122 (33 percent) cases 
involved the use of a narcotic-acetaminophen prescription product, and 
76 (21 percent) cases reported use of an OTC single ingredient 
acetaminophen product. Approximately 25 percent of all adult cases 
reported use of more than one acetaminophen product. When more than one 
acetaminophen product was reported, a narcotic-acetaminophen 
prescription product in combination with an OTC product containing 
acetaminophen was used more often than any other

[[Page 77321]]

combination of acetaminophen products. These cases also used higher 
doses than people who took only one acetaminophen-containing product.
    Dosing amounts were reported in 132 of the 282 adult cases. The 
mean and median daily dose were 6.5 and 5 g, respectively, but ranged 
from 650 mg to 30 g/day. Where the dosage strength was known, 500 mg 
acetaminophen was reported most often. If a dose range was reported in 
the case, the mid-point was used in the analysis. If the strength was 
unknown, a 500-mg strength was assumed. Dosing in the 65 adults with 
severe liver injury from this group showed a mean and median daily dose 
of 7.1 and 6.23 g, respectively. Twenty-three of the 65 cases with 
severe liver injury reported doses of less than 4 g/day. People who 
used more than one acetaminophen product reported taking higher doses 
than people who took a single product. Qualitative dosing information 
was provided for an additional 43 (15 percent) cases with terms such as 
``excessive doses'' or ``recommended doses.'' Two out of three of these 
cases suggest that greater than recommended doses were used.
    Alcohol use was reported in 116 of the adult cases and the content 
of the reports was highly variable. Alcohol use in these cases was 
defined by FDA as alcoholism or alcohol abuse in 64 cases; regular, 
daily, or moderate use in 23 cases; occasional use in 10 cases; 
previous use in 6 cases; and 13 cases did not provide a description. 
Eighty-six (74 percent) of the 116 alcohol users developed severe liver 
injury. For those cases with acetaminophen dose information, the mean 
dose associated with toxicity was lower for alcohol users compared to 
nonalcohol users (table 7).

                                  Table 7.--Acetaminophen Dose and Alcohol Use
----------------------------------------------------------------------------------------------------------------
     Category of Liver Disease (Developed Post-
                   Acetaminophen)                       Alcohol Users (Mean Dose)       Non-Users (Mean Dose)
----------------------------------------------------------------------------------------------------------------
All (N=132)                                                           5.6 g (N=53)                  6.9 g (N=79)
----------------------------------------------------------------------------------------------------------------
Severe only (N=65)                                                    6.0 g (N=38)                  8.6 g (N=27)
----------------------------------------------------------------------------------------------------------------

    A history of prior liver disease, or possible underlying liver 
disease, was reported in 70 cases. In at least 20 of these cases, the 
pre-existing liver disease was reportedly due to alcohol. Twenty-three 
people reported a history of, or possible, viral hepatitis. Among the 
70 cases with pre-existing liver disease, 49 percent (70 percent) 
developed severe liver injury. Table 8 shows the dose that was 
associated with liver injury for cases with and without pre-existing 
liver disease. The first row includes all cases (all degrees of acute 
liver injury) that reported dosing information. The second row shows a 
dose comparison in people who experienced severe liver injury after 
acetaminophen exposure.

                                 Table 8.--Acetaminophen Dose and Liver Disease
----------------------------------------------------------------------------------------------------------------
  Category of Liver Injury Associated With      Cases With Pre-existing Liver   Cases With No Pre-existing Liver
            Acetaminophen Dosing                     Disease (Mean Dose)               Disease (Mean Dose)
----------------------------------------------------------------------------------------------------------------
All (N=132)                                                       5.4 g (N=36)                      6.8 g (N=96)
----------------------------------------------------------------------------------------------------------------
Severe only (N=65)                                                5.7 g (N=23)                      7.8 g (N=42)
----------------------------------------------------------------------------------------------------------------

    Some additional factors may have contributed to the development of 
hepatotoxicity in these adults. Use of other medications that may have 
contributed to hepatotoxicity was reported in 93 cases, including 63 
cases that involved products that are labeled with warnings about 
potential hepatotoxicity. A small number of reports also mentioned the 
existence of concomitant malnutrition or decreased oral intake.
    FDA noted that there are limitations to interpreting the AERS data. 
Dosing information may be unreliable. Acetaminophen products are 
generally taken on an as-needed basis, so the actual dose ingested can 
be difficult to ascertain. There is no certainty that all of the adult 
cases included in this analysis were unintentional. Stigma may be 
associated with reporting suicide, so cases may be reported as 
unintentional when they were intentional overdoses. In addition, 
spontaneous reporting systems cannot provide certainty that 
acetaminophen was the cause of any of the reported adverse event. 
Furthermore, incidence rates cannot be determined, because the 
numerator or denominator descriptors for the entire population are not 
available. Overall, spontaneous reports may be subject to significant 
underreporting.
    The AERS cases strongly suggest that particular circumstances were 
likely to have led to hepatotoxicity. Some examples of those 
circumstances follow:
     Errors related to product confusion were mostly observed 
in pediatric cases. These errors primarily involved confusion over 
varying product formulations and strengths and use of inappropriate 
measuring devices.
     Many adults were taking more than the recommended dose of 
acetaminophen and, in some cases, use of multiple products likely 
contributed to hepatotoxicity.
     Risk factors, such as alcohol use or pre-existing liver 
disease, were identified and may have increased the risk for 
hepatotoxicity.
    FDA presented NDAC with several questions that remained unaddressed 
by FDA's review:
     Do users lack knowledge of the potential for and symptoms 
of hepatotoxicity when using a product containing acetaminophen?
     Does malnutrition or fasting affect severity of 
hepatoxicity?
     What is the contribution of concomitant hepatotoxic 
medication?
     What additional factors place a small number of 
individuals at risk for severe hepatotoxicity at various dose levels 
(i.e., under, at, or above the recommended dose)?
    It is clear that unintentional acetaminophen doses are associated 
with a large number of emergency department and hospital admissions and 
are related to an estimated 100 deaths each year. Using a number of 
data sources, analyses have shown that circumstances leading to

[[Page 77322]]

acetaminophen hepatotoxicity are multifactorial. FDA asked the 
committee to consider the contribution of each of the following in 
producing unintentional overdose toxicity:
     Product--the ingredient is present in multiple 
prescription and OTC drug products and in multiple oral formulation 
strengths
     Knowledge--since a number of cases have occurred from 
multiple product use and overuse, there is likely a lack of knowledge 
about safe use of acetaminophen
     Risk factors--multiple data sources identify alcohol and 
underlying liver disease as risk factors that may increase the 
potential for hepatotoxicity.
    Several drug manufacturers and other interested parties provided 
additional comment (Ref. 4):
     One major manufacturer of acetaminophen OTC drug products 
provided the following comments:
    1. The precise incidence of harmful, unintentional overuse cannot 
be accurately determined from the current databases. Forty-eight 
million American adults use products containing acetaminophen in any 
single week; thus, harm is rare and is caused by inadvertent overdose.
    2. There are limitations to the AERS data set for assessing hepatic 
events. Patients consistently underestimate the dose taken, and suicide 
attempts are often not recorded in patients who are found unconscious 
or intoxicated. The AERS reports found to be definitely associated with 
acetaminophen involved substantial overdose in individuals with self-
abusive behaviors (e.g., alcohol abuse, bulimia). Causality cannot be 
ascertained using retrospective data, especially case reports, because 
the dose history is often inaccurate.
    3. Formulations most commonly reported were OTC single-ingredient 
and prescription combination acetaminophen products. OTC acetaminophen 
combination products were rarely reported.
    4. Serious hepatotoxicity occurs following substantial overdose (a 
single dose of approximately 15 g or use of approximately 12 g for 
multiple days).
    5. FDA focused on unintentional misuse. The manufacturer noted they 
had implemented labeling changes to minimize the inadvertent overuse of 
analgesics. The manufacturer recommended an organ specific overdose 
warning.
     One manufacturer of ibuprofen OTC drug products provided 
the following comments:
    1. In overdose situations, in any given year, the number of deaths 
for acetaminophen reported by the AAPCC is approximately 20 times that 
for ibuprofen.
    2 . Unintentional overdose of acetaminophen can put consumers in a 
life-threatening situation due to the delayed onset of clinical 
symptoms of toxicity.
    3. Advertising portrays acetaminophen as a totally safe ingredient. 
This portrayal may exacerbate use and contribute to the silent danger 
resulting from overdose.
     One individual presented a review of acetaminophen 
overdose admissions at the University of Pennsylvania hospital over a 
4-year period. Fifty-four reports of acetaminophen overdose were found 
in the hospital's database. Of the 47 cases reviewed to date, 23 (50 
percent) were reported to be unintentional overdoses. In 13 of these 23 
cases, the reviewer was able to document that an attending physician or 
a psychiatry consultant concluded that there had been no suicidal 
intent.
    1. The median and average doses were between 6 and 8 g/day. These 
values are above the recommended maximum daily dose (4 g/day), but 
below the 10 to 15 g dosage usually considered to be toxic. There were 
three cases of intentional overdose and three cases of unintentional 
overdose involving prescription acetaminophen products. OTC products 
were associated with 20 intentional and 21 unintentional overdoses. 
More patients in the unintentional overdose group used single 
ingredient acetaminophen (i.e., not a combination product). The primary 
reason reported for exceeding the maximum dose was to treat unrelieved 
pain. Many patients stated that they knew they were exceeding the 
recommended dose and did so because they thought it was a safe drug. 
Thirty percent of the patients used the drug over a period of greater 
than 7 days.
    2. The unintentional overdose group experienced greater morbidity 
and mortality than the intentional overdose group. The peak 
acetaminophen levels in the intentional overdose group were much lower 
compared to the unintentional overdose group (27.8 versus 115.1 mg/L). 
The unintentional overdose group had much higher peak levels of Alanine 
aminotransferase (ALT) (5,193 versus 3,065 units/L), Aspartate 
aminotransferase (AST) (6,819 versus 2,742 units/L), International 
Normalized Ratio (INR) (4 versus 2.5), and total bilirubin (5.87 versus 
1.87 mg/dL). Patient outcomes were generally worse in the unintentional 
overdose group, in which more patients failed to have resolution of the 
liver problems from the overdose (31 versus 4 percent). More patients 
were evaluated for transplants (11 versus 9), received transplants (2 
versus 0), and died (3 versus 0) as a result of unintentional 
overdoses.
    3. Compared to the intentional overdose group, the unintentional 
overdose group was more likely to have one or more of the following 
risk factors for acetaminophen toxicity: (1) Hepatic disease, (2) acute 
or chronic alcohol use, (3) drug abuse, or (4) concomitant disease. 
Ninety-six percent of cases in the unintentional overdose group had one 
or more of these risk factors, as compared to 70 percent in the 
intentional group. Acute and chronic alcohol use was present in 87 
percent of unintentional overdose cases, as compared to 61 percent of 
the intentional overdose cases. Thus, the existence of risk factors may 
have an impact on toxicity in unintentional ingestions.
     One individual described the untimely death of her son who 
initially used a prescription product. When the prescription was 
finished, he purchased an OTC acetaminophen product and developed flu 
like symptoms. Another OTC acetaminophen product was subsequently used 
to treat the flu symptoms, resulting in hepatotoxicity. He was 
hospitalized and ultimately died.
     A professional pharmaceutical association encouraged 
consumers to carefully read product labeling. The association also 
recommended: (1) Clear labeling on all prescription and OTC drug 
products containing acetaminophen with special statements (e.g., 
``contains acetaminophen'' on the product's PDP), and (2) pharmacists 
placing auxiliary labels on the vial of prescription drug products 
containing acetaminophen to identify this ingredient.
     A consumer public health organization described a consumer 
survey showing that many consumers do not recognize the potential for 
harm from: (1) Taking more than the recommended dose, (2) taking more 
than one product containing acetaminophen, or (3) inappropriately 
combining OTC and prescription drug products containing acetaminophen.
     A member of a national health foundation expressed concern 
that present marketing practices make it very difficult to find the 
standard 325-mg acetaminophen dosage unit. As a result, many consumers 
believe that the 500-mg product is the only one available. This failure 
to more broadly market the lower dose may contribute to increased 
adverse events. The individual

[[Page 77323]]

advocated educational efforts to help minimize this problem.
     A spokesperson for a national consumer organization 
described marketing limitations that are employed in the United Kingdom 
and intended to limit the potential for overdose. In September 1998, a 
restriction was placed on the number of tablets in acetaminophen 
packages for sale without a prescription. If sold in a supermarket, the 
maximum is 16 tablets per package. If sold in a pharmacy, the maximum 
is 32 tablets per package. There is also an overall restriction that a 
maximum of 100 tablets can be purchased at one time. The representative 
stated that early evaluations of this program have shown decreases in 
(1) total and severe acetaminophen overdoses and (2) overdoses related 
to liver transplant and death.
    Several drug manufacturers and others submitted additional 
information for the committee to review (Ref. 5):
     One major manufacturer of acetaminophen OTC drug products 
provided the following comments (Ref. 5, Tab A):
    1. AERS serves as a signal generating system for rare, unexpected 
adverse events in marketed products. It cannot be used to determine 
event rates, dose ingested, or patient dosing intent.
    2. FDA's review of the AERS data set was intended to exclude 
obvious suicide, usually associated with very large drug ingestion. 
Thus, the reported dosage (which could only be estimated in 48 percent 
of the reports in the data set) is skewed significantly toward labeled 
directions for use, so cases may falsely appear to be consistent with 
inadvertent misuse.
    3. The selective data in FDA's AERS review cannot be used to 
determine an acetaminophen toxicity threshold associated with any 
patient condition (i.e., concomitant drug, alcohol history, or pre-
existing concomitant disease).
    4. The quality of the 281 adult reports in AERS was evaluated by 
the manufacturer. The manufacturer concluded that 168 reports (24 
percent) contained insufficient information to estimate the dose taken 
and 212 reports (88 percent) contained no liver pathology information. 
AST and ALT levels were not reported in 108 cases (38 percent). Only 61 
reports (25 percent) had information about viral hepatitis testing and, 
of these, 29 reports were positive for hepatitis A, B, or C.
    5. There are flaws in the derivation of FDA's theory that alcohol 
use, underlying/history of liver disease, and potentially the use of 
hepatotoxic concomitant medications, may increase susceptibility to 
acetaminophen-associated hepatotoxicity at unexpectedly low doses of 
acetaminophen. The manufacturer provided arguments that the existence 
of any of these factors in a case report may each inherently interfere, 
for various reasons, with establishing the correct assessment of a 
hepatotoxic dose of acetaminophen.
     An expert panel sponsored by a manufacturer of 
acetaminophen products reviewed all 281 adult reports in AERS and 
assigned a probability category relating the reported hepatic adverse 
events to acetaminophen exposure. In 3 reports the adverse event and 
exposure were considered ``definitely'' related, in 74 reports they 
were ``probably'' related, 47 reports they were ``possibly'' related, 
in 53 reports they were unlikely to be related, and in 27 reports they 
were definitely not related. Data were considered insufficient in 73 
reports, 3 reports were not able to be evaluated and there was no 
consensus regarding the evaluation of 1 report.
    Based on an assessment of several databases, a sponsor calculated 
that the worst case scenario of deaths from acetaminophen overdose is 
estimated to be 213 deaths per year (Ref. 5, Tab A).
     One manufacturer submitted an analysis of data from TESS 
(Ref. 5, Tab B). The manufacturer made the following conclusions from 
these data:
    1. The majority of hepatotoxicity cases (65 percent of cases in the 
year 2000) involved use of one acetaminophen-containing analgesic 
product.
    2. Acetaminophen-containing cough/cold medications were not a 
significant contributor to the total number of reports of acetaminophen 
associated hepatotoxicity (2 percent of cases in the year 2000).
    3. Only 1 percent of the reported cases of hepatotoxicity in 2000 
involved use of an OTC acetaminophen-containing cough/cold product 
concomitantly with other acetaminophen-containing product(s).
     One physician stated that 3 to 4 g of acetaminophen per 
day is the upper range of a safe dose (Ref. 5 Tab C). For an individual 
who is a regular user of alcohol, in a prolonged fasting or in a rapid 
weight loss program, the upper limit of a safe dose is unknown, but 
unlikely to not exceed 2 g of acetaminophen. No data were provided to 
support these observations.
     Several organizations urged that labeling be improved to 
provide clear directions about the appropriate doses for use and 
frequency of administration, especially for combination products (Ref. 
5 Tab D). Consumers need to know the type of medication and the dose of 
OTC analgesic in every combination product to ensure safe and effective 
use.
3. NDAC Deliberations and Recommendations Concerning Acetaminophen
    NDAC unanimously agreed that the evidence of risk associated with 
unintentional overdose of acetaminophen warrants FDA labeling changes, 
without awaiting the outcome of further studies. NDAC noted the 
following four major areas of concern:
    1. Unintentional use of multiple acetaminophen containing products
    2. Exceeding the recommended dose without recognizing the 
consequences
    3. Improper dosing of infants
    4. The unknown consequences of use in special populations, such as 
alcohol abusers.
    NDAC recommended that the minimum requirements for change should 
include, for all products containing acetaminophen (including those 
available by prescription), the addition of distinctive labeling 
(highlighted or bold type) on the front panel or PDP to state that the 
products contain acetaminophen. FDA noted that the nonproprietary name 
of prescription drugs must appear in labeling in letters at least half 
the size of the brand name (see 21 CFR 201.10(g)(2)). NDAC recommended 
that a similar provision also be applied to OTC drug products 
containing acetaminophen, such as a standard to ensure prominence of 
important information. NDAC stated that consumers need to be informed 
that combining products containing acetaminophen can result in 
exceeding the recommended dose.
    NDAC commented that there are insufficient data in the OTC setting 
on risk management, understanding consumer behavior, and the 
effectiveness of warnings on labels. This lack of data makes it 
difficult to determine which factors contribute to liver injury. 
Although these factors are not clearly understood, NDAC concluded that 
labeling revisions are needed to help minimize any risks.
     Separate liver toxicity and alcohol warnings. NDAC 
recommended a liver toxicity statement, separate from the alcohol 
warning, be added to the label so that the potential for liver toxicity 
would not appear to be applicable only to consumers who drink alcohol. 
NDAC noted that alcohol is not the only risk factor for hepatotoxicity. 
It was also felt to be important to warn consumers of the consequences 
of taking multiple products containing acetaminophen and that toxicity 
can be related to the total

[[Page 77324]]

dose of acetaminophen taken during a given period of time. NDAC felt it 
would be more prudent to describe these risks in a separate warning to 
more fully inform consumers who do not abuse alcohol.
    NDAC did not propose exact language. It was believed that it was 
important that the message not refer to ``overdose,'' but rather to a 
statement such as ``do not take more'' or ``do not exceed the 
recommended dose.'' NDAC believed that the term ``overdose'' would not 
be understood to be pertinent to consumers whose intent was to use the 
product safely. One NDAC member stated the term ``exceed'' is not part 
of consumers' common vocabulary and proposed that it would be more 
useful to inform consumers of a specific allowable total dose (e.g., 
not to take more than a specified number of tablets in a given period).
    NDAC re-examined the currently required alcohol warning for 
acetaminophen, which states: ``Alcohol Warning: If you consume 3 or 
more alcoholic drinks every day, ask your doctor whether you should 
take acetaminophen or other pain relievers/fever reducers. 
Acetaminophen may cause liver damage.'' NDAC inquired why ``three 
drinks'' were used in the alcohol warning. FDA responded that the 
number is from recommendations of the American Heart Association as to 
what constitutes excessive alcohol use. FDA stated that it recognized 
this may seem arbitrary and asked NDAC to provide further 
recommendations. NDAC questioned whether doctors are well-informed with 
proper information about the relationship between alcohol and 
acetaminophen use and whether educational efforts should also include 
educational efforts directed at health care professionals and 
consumers. NDAC was concerned about the lack of available data on which 
to base such advice, noting that there is a lack of information about 
how to determine the amount of alcohol that may be harmful to any 
individual. NDAC noted that reducing the risk of drug adverse events is 
the goal, but believed that more data are essential for them to make 
specific recommendations.
    FDA asked NDAC to comment on whether the current maximum allowable 
daily dose of acetaminophen should be used by individuals consuming 
three or more drinks per day. One NDAC member agreed that was prudent 
to lower the dose, however, the majority of NDAC members believed that 
more information is needed before dose reductions could be implemented 
for this population. NDAC stated that, intuitively, a lower dose would 
decrease potential toxicity, but noted that there is a lack of 
information to support such labeling.
    One NDAC member mentioned that although some evidence appeared to 
show an association of increased acetaminophen toxicity for patients 
with pre-existing liver disease, this finding is contrary to 
hepatologists' experience with acetaminophen. Generally, acetaminophen 
is considered safe for use in patients with liver disease, including 
people awaiting liver transplantation. Most hepatologists recommend 
acetaminophen for such patients, but at reduced doses, such as 2 g 
maximum in a 24-hour period. NDAC urged more studies, not only of risk 
factors, but of a plan to reduce risk.
     Consumer and healthcare provider education. NDAC concluded 
that FDA and manufacturers have a joint responsibility to reduce the 
occurrence of unintentional overdoses from acetaminophen. NDAC 
considered it essential that consumer and professional educational 
programs heighten awareness of the risk, particularly to certain 
populations. NDAC believed consumers are unfamiliar with the term 
``acetaminophen'' and are more likely to know the brand names. NDAC 
stated that an effort should be made to create a broader educational 
campaign to inform consumers that acetaminophen is an analgesic, 
because most people are familiar with aspirin and not with 
acetaminophen. NDAC also suggested that the packaging, display, format, 
and wording recommendations in OTC drug product labeling should also be 
extended to all product advertisements, both in print and media, 
because advertising is an educational tool for many consumers.
    NDAC stated that many physicians and pharmacists may not be aware 
of the risks of unintentional overdose. NDAC added that, along with 
consumer education, professional programs are important, because 
prescription products containing acetaminophen are widely used. 
Education of pharmacists would be needed to support the use of 
additional labeling information (stick-on labels, etc.) attached to 
prescription containers. NDAC stated that auxiliary labeling is 
critical to conveying information that the prescription product 
contains acetaminophen.
     Pediatric dosage. NDAC also expressed concern about the 
lack of standardized pediatric dosage information, especially for 
infants under 2 years of age. FDA stated that a separate rulemaking on 
this issue was in progress and will be addressed in a future Federal 
Register publication.

C. Aspirin and Other NSAIDs

    On the second day of the meeting (September 20, 2002), NDAC 
considered safety issues related to the use of aspirin and other OTC 
NSAIDs. The primary areas for discussion included the potential for GI 
bleeding and renal toxicity from using these drugs. The prescription 
labeling for NSAIDs and the professional labeling for aspirin have 
warnings for GI bleeding and possible renal toxicity. Aside from the 
alcohol warning required on all OTC NSAID drug products, current OTC 
labeling does not have warnings about damage to specific organs.
1. Points for Discussion
    FDA asked NDAC to consider the relative risks for GI bleeding and 
renal toxicity associated with OTC doses of NSAIDs, including aspirin, 
and to consider the following issues:
     How should the relative risk of GI bleeding or renal 
toxicity be described to consumers who use the maximum recommended 
daily OTC dose?
     Are there subpopulations of consumers who are at a greater 
risk for developing GI bleeding or renal toxicity with OTC doses?
     If additional warnings are recommended, should such 
warnings inform consumers about the risk, provide information on the 
at-risk populations, or provide expanded information to all consumers 
about symptoms of toxicity?
     Should the warnings that are currently in professional 
labeling for aspirin be conveyed to consumers as part of the OTC 
labeling?
     If yes, which warnings should be conveyed and how should 
they appear in OTC drug product labeling?
     Are any additional studies needed to evaluate 
subpopulations at risk for serious adverse events, labeling revisions, 
and any other issues?
     Should the labeling and packaging of these products more 
prominently state that the product contains aspirin or the specific 
NSAID?
2. Presentations and Submissions to NDAC
GI bleeding
    FDA staff described cases of GI bleeding (spontaneous reports from 
AERS received by FDA between 1998 and 2001) in individuals who used OTC 
NSAIDS (including aspirin) as an analgesic and/or antipyretic (Ref. 8). 
The review was limited to cases that mentioned ``OTC'' in the narrative 
of the report. Any cases that appeared to involve prescription NSAID 
products were excluded. A total of 279 cases of

[[Page 77325]]

GI bleeding were included: 82 for aspirin and 197 for nonaspirin NSAIDs 
(i.e., ibuprofen, ketoprofen, and naproxen). The mean age was 59 years 
(ranging from 1 to 99 years). There were 138 (49.5 percent) males, 119 
(42.7 percent) females, and 22 cases (7.9 percent) in which gender was 
not reported.
    Cases that specified the location in the GI tract of the bleed 
included: Stomach (63 cases), duodenum (35 cases), unspecified upper GI 
site (15 cases), esophagus (13 cases), and rectum/colon/small intestine 
(9 cases). For nonaspirin NSAIDs, the median time to onset was 7 days. 
Time to onset was defined as the time between each person's first use 
of the drug and the time that bleeding occurred. For aspirin, time to 
onset was about 30 days. For both aspirin and nonaspirin NSAIDs, there 
was a wide range in time to onset. FDA reviewed the cases for common 
risk factors for GI bleeding that are recognized in the medical 
literature, including previous GI bleed or history of an ulcer, social 
history (alcohol or tobacco use), concomitant use of other drugs 
(NSAIDs, aspirin, anticoagulants, corticosteroids), use of doses higher 
than recommended, and advanced age (65 years and older). The results 
included 195 (70 percent) cases with at least one risk factor, 112 (40 
percent) cases with more than one risk factor, and 81 (29 percent) 
cases with no risk factors apparent in the report. The most commonly 
reported risk factors were:
     Concomitant use of another NSAID or aspirin (50 percent)
     Advanced age (40 percent)
     History of a previous GI bleed (18 percent)
     Using NSAID doses above the recommended OTC dose (14 
percent)
     Alcohol or tobacco use (5 percent).
    In the aspirin cases, only one person was reported to have exceeded 
the OTC recommended dose. Of the 279 aspirin and nonaspirin cases, 212 
people (76 percent) were hospitalized. Most recovered; however, 13 (4.7 
percent) people died.
    FDA indicated that these reports suggest that serious GI bleeding 
events can occur with NSAID and aspirin use at OTC dosage strengths, 
within the duration of use described in the OTC labeling.
    Dr. Byron Cryer, of the University of Texas Southwestern Medical 
School, provided an overview of the GI risks from NSAID use (Ref. 9). 
His review was not limited to OTC dosing of NSAIDs and extended to all 
NSAIDs. He made the following points:
     Despite the overall decrease in prevalence of 
uncomplicated ulceration, the incidence of complicated ulcerations 
(specifically, bleeding ulcers) has increased in the past few years. 
This is likely due to increased NSAID exposure, possibly from OTC use. 
Gastric ulceration (15 percent prevalence) associated with NSAIDs (at 
recommended doses) is much more common than duodenal ulceration (5 
percent prevalence). Clinically relevant ulceration (i.e., ulcers that 
present with bleeding), has a prevalence of approximately 2 percent.
     A history of prior bleeding, anticoagulant use, 
corticosteroid use, and increasing age are factors that increase the 
risk of bleeding associated with NSAIDs (Refs. 10 through 13).
     The prevalence of upper GI bleeding from aspirin use is 
different than for nonaspirin NSAID use. A study evaluated the 
prevalence of aspirin and nonaspirin NSAID use in 421 patients 
evaluated for upper GI bleeding (Ref. 14). Patients were asked at the 
time of hospital admission whether they were using prescription or OTC 
products and whether they were using nonaspirin NSAIDs or aspirin. The 
results show that 42 percent of GI bleeding was associated with aspirin 
use. Fourteen percent of patients admitted to the hospital were using 
prescription NSAIDs and 9 percent were using OTC NSAIDs.
     A recent study suggests that up to 80 percent of people 
with GI bleeding are taking an NSAID, primarily low dose aspirin (Ref. 
15). The relative risk (RR) (i.e., the probability of an event in the 
active group divided by the probability of the event in the control 
group) was 2.4 for a low/medium NSAID dose and 4.9 for a high dose.
     Another study compared the use of OTC aspirin, ibuprofen, 
naproxen, and acetaminophen between two case groups, one group who 
experienced GI bleeding events and a control group of cases who did not 
experience GI bleeding (Ref 16). The patients in the GI bleeding group 
were more likely to be taking aspirin or OTC NSAIDs prior to the GI 
bleeding event than were patients in the control group. The extent of 
use of acetaminophen was comparable between the two groups. This study 
included people with chronic disease and chronic analgesic exposure, 
providing information about a subgroup of patients that may be 
different from relatively healthy individuals exposed to OTC analgesics 
for acute, short-term, or intermittent use.
     The risk of combining low dose aspirin with nonaspirin 
NSAIDs was examined in a large national cohort study in Denmark (Ref. 
17) in which 27,000 people were given 100 to 150 mg aspirin every day. 
The study showed that there is an increased risk of upper GI bleeding 
in patients who combine low dose aspirin and other NSAIDs compared to 
the incidence of GI bleeding events in the general population (RR 5.6; 
95% confidence interval (CI) 4.4--7.0). The risk of GI bleeding among 
patients taking more than one NSAID was approximately double the risk 
among patients taking aspirin alone.
     In an American College of Gastroenterology Bleeding 
Registry (Ref. 18), cases of GI bleeding were assessed for use of 
aspirin or OTC NSAIDs and concomitant use of alcohol. These cases were 
compared to data from a control cohort of cases with no GI bleeding. 
The results suggest an increased risk of bleeding when alcohol is used 
while taking an OTC NSAID (odds ratio 4.47; 95 percent CI 2.73 -7.32) 
compared to the use of either alcohol or OTC NSAIDs alone (odds ratio 
for alcohol alone 2.07; 95 percent CI 1.48--2.88/ odds ratio for NSAID 
alone 2.76; 95 percent CI 2.03--3.74). Dr. Cryer noted that the results 
of the study were confounded because 12 percent of the subjects in the 
registry had gastric or esophageal varices (enlarged veins). He 
suggested that there may be an increased risk particularly to patients 
with an extensive history of alcohol use who are exposed to OTC NSAIDs.
     Another report (Ref. 19) evaluated subjects who regularly 
or occasionally used aspirin or ibuprofen and compared the RR of GI 
bleeding between those who never used alcohol and those who used 
alcohol. The results suggest a modest increase in RR of upper GI 
bleeding in alcohol users; however, the statistical analyses did not 
provide a strong distinction between alcohol users and non-users.
    Dr. Marie Griffin of Vanderbilt University discussed additional 
information obtained from large population studies regarding GI 
complications associated with the use of NSAIDs (Ref. 20). She made the 
following points:
     The risk of ulcer disease was shown to increase 10-fold in 
older people and this risk is increased further by use of NSAIDs (Ref. 
21). This ulcer hospitalization study found the absolute risks to 
increase from approximately 4 hospitalizations per 1,000 person-years 
in older non-users of NSAIDs to approximately 16 hospitalizations per 
1,000 person-years in older users of NSAIDs. In general, consumers 
taking NSAIDs for a year at moderate doses have about a 1 to 2 percent 
chance of being hospitalized with a complication.

[[Page 77326]]

     The risk of hospitalization for peptic ulcer disease 
(PUD), and risk of GI complications, increases with increasing NSAID 
doses (Refs. 20, 22, and 23).
     Data obtained from the Tennessee Medicaid database 
indicate that the greatest absolute risk for hospitalization for PUD 
occurs in the first 30 days of NSAID use among patients older than 65 
years of age (Ref. 23). For older patients, there were 26.3 
hospitalizations for PUD per 1,000 NSAID users per year within 30 days 
of starting NSAID therapy, 20.9 hospitalizations between 31 and 180 
days of use, and 16.2 hospitalizations for use longer than 180 days. In 
contrast, there were 4.2 hospitalizations per 1,000 NSAID non-users per 
year. Overall, people of all ages have a 1 to 2 percent chance of being 
hospitalized with a complication when using NSAIDs for over a year at 
moderate doses.
     Surveys in the 1980s showed that approximately 1 to 3 
percent of people 65 and older take a prescription corticosteroid drug. 
The concomitant use of an OTC NSAID with a corticosteroid increases the 
risk of ulcer complication 13- to 15-fold over NSAID non-users. The 
ulcer hospitalization rate in people using both drugs was about 5 to 6 
per 100 people per year.
     In the 1980s, 1 to 2 percent of the elderly population 
were co-prescribed warfarin (an anticoagulant drug) and NSAIDs. The 
risk of GI bleeding increased by 12 fold in patients who used both 
therapies compared to NSAID non-users. The risk of hospitalization for 
GI bleeding is approximately 3 per 100 per year in patients who use 
warfarin and NSAIDs.
    Several drug manufacturers and others provided additional comments 
(Ref. 4):
     One drug manufacturer of ibuprofen OTC drug products 
stated that the OTC ibuprofen daily regimen is 1,200 mg/day versus 
2,400 to 3,200 mg a day for prescription use. Unlike acetaminophen, the 
OTC directions clearly state to take one 200-mg tablet and, only if 
necessary, a second tablet may be taken. OTC use of NSAIDs is limited 
to a maximum of 10 days, whereas prescription use is chronic.
     One drug manufacturer stated that each analgesic 
ingredient requires appropriate labeling for its pattern of use and 
that it is inappropriate to label OTC products with risks associated 
with chronic, long-term prescription dosing. The prescription and OTC 
uses of NSAIDs are distinct and these two dose levels have different 
risk-benefit profiles. The OTC use is short-term for pain relief and 
fever reduction, with a low risk. Results of prevention studies of 
secondary and acute myocardial infarction have shown that for people 
whose 10-year risk of having a subsequent cardiovascular event is 
between 20 and 50 percent, the cardiovascular benefit of aspirin far 
outweighs the risks. The relative and absolute risks of aspirin are 
low.
     One consumer advocacy organization stated that GI bleeding 
caused by NSAIDs (reference to prescription or OTC products was not 
specified) is now recognized as the most common serious adverse drug 
reaction in the United States and accounts for as many as 16,000 deaths 
a year. The organization requested that: (1) Product labeling contain a 
clear organ-specific warning about GI bleeding, (2) packaging include 
consumer education on GI bleeding, such as a leaflet inside the 
packaging listing specific symptoms and factors associated with 
increased risk, and (3) a separate warning, about increased risk of GI 
bleeding associated with alcohol use, be added and directed at 
consumers who drink some alcohol.
    Several drug manufacturers submitted additional information (Ref. 
5):
     One manufacturer stated that the safety profile for OTC 
ibuprofen, generated over 18 years of OTC use by millions of consumers, 
indicates that the current labeling has been effective in informing 
consumers of the appropriate use of the drug (Ref. 5, Tab E). The 
manufacturer stated that FDA has received an average of 18 reports per 
year of GI perforations, ulcers, or hemorrhage associated with OTC use.
     One manufacturer stated that no antidote is available for 
aspirin or ibuprofen overdose (Ref. 5 Tab F). Acute overdose and 
chronic aspirin toxicity are associated with significant morbidity (as 
high as 25 percent). If acetaminophen was restricted, aspirin and other 
NSAID use would increase. Available data suggest that more people would 
die from aspirin and other NSAID-related GI bleeding. The net public 
health impact of changing labeling for OTC IAAA drug products should be 
taken into consideration in the formulation of any regulatory policy.
     One manufacturer stated that the risk patterns associated 
with use of acetaminophen and aspirin are distinct from one another and 
support different product labeling for the various ingredients in OTC 
IAAA drug products (Ref. 5, Tab G). There are no data to support the 
view that a balanced warning for acetaminophen will cause a significant 
number of patients to switch to another OTC analgesic. Available data 
indicate that both the absolute number, and the rate (per billion 
tablets sold), of fatalities associated with acetaminophen overdose in 
the United States significantly exceeds the corresponding figures for 
aspirin overdose.
     One manufacturer stated that the occurrence of GI adverse 
events with naproxen/naproxen sodium at single low dose (220 mg), at 
multiple doses (up to 880 mg), and as needed OTC doses, are comparable 
to the occurrence associated with use of placebo (Ref. 5, Tab H). 
Nausea, dyspepsia, and vomiting are the most common GI adverse events.
Renal effects
    FDA staff presented information about the potential for OTC NSAIDs 
to cause nephrotoxicity (Ref. 24) and made the following points:
     NSAID-induced nephrotoxicity at prescription doses is 
characterized by fluid and electrolyte disturbances leading to sodium 
retention, edema (accumulation of watery fluid in cells and tissues), 
and hyperkalemia (high concentration of potassium in the blood). These 
drugs can also cause blood pressure to increase. The majority of 
healthy people who are exposed to therapeutic doses of NSAIDs for a 
limited time tolerate these drugs without untoward renal effects. Some 
subsets of the population are more susceptible to potentially life-
threatening nephrotoxicity (e.g., acute renal failure and serious fluid 
and electrolyte disorders), including people who have volume depletion, 
underlying kidney disease, congestive heart failure, or liver 
dysfunction with ascites (accumulation of fluid in the peritoneal 
cavity of the abdomen), and the elderly. The use of NSAIDs in the last 
trimester of pregnancy has been associated with significant neonatal 
nephrotoxicity.
     Ideally, an assessment of the nephrotoxic risk associated 
with OTC NSAIDs should rely on data derived from prospective, 
randomized, placebo-controlled and adequately powered studies in 
healthy, as well as at-risk, populations. However, such data are not 
available. In 1995, the National Kidney Foundation (NKF) convened a 
group of investigators and clinicians to consider and develop 
recommendations on the issue of analgesic-related kidney disease. The 
database used to make their recommendations was comprised of 556 
articles published in the medical literature on aspirin, acetaminophen, 
aspirin-acetaminophen combinations, and NSAID-related nephrotoxicity. 
The NKF recommended ``[t]here should be an explicit label warning 
people taking over-the-counter NSAIDs of the potential renal risks of 
consuming the drugs.''

[[Page 77327]]

     FDA staff identified all cases in the AERS database 
reporting acute renal failure, chronic renal failure, and renal failure 
in association with the use of OTC doses of NSAIDs. The time period 
reviewed was from the OTC approval date for ibuprofen (1984), naproxen 
sodium (1994), and ketoprofen (1995) through August 10, 1999. FDA's 
review included cases that specified that either OTC dosages and/or an 
OTC NSAID product had a role in the adverse reaction. People with pre-
existing conditions were not included. Table 9 shows the number of 
cases of renal failure reported, including 94 cases for ibuprofen, 26 
cases for naproxen sodium, and 1 case for ketoprofen. Fifty-six people 
who used ibuprofen required hospitalization; nine needed dialysis; and 
nine died. Renal failure occurred within less than 7 days of exposure 
to the drug. Fourteen ibuprofen cases were within the pediatric age 
group. For naproxen sodium, 25 people were hospitalized, 4 required 
dialysis, and 3 died. The single ketoprofen case was hospitalized.

                        Table 9.--FDA AERS Cases of Renal Failure at OTC Doses of NSAIDs
----------------------------------------------------------------------------------------------------------------
                                  Ibuprofen                  Naproxen Sodium                 Ketoprofen
----------------------------------------------------------------------------------------------------------------
Reporting Period                            15 years                       5 years                       4 years
----------------------------------------------------------------------------------------------------------------
Renal Failure Cases--                             94                            26                             1
 Total
----------------------------------------------------------------------------------------------------------------
Renal Failure Cases--                             80                            26                             1
 Adult
----------------------------------------------------------------------------------------------------------------
Renal Failure Cases--                             14                             0                             0
 Pediatric
----------------------------------------------------------------------------------------------------------------

    Next, Dr. Griffin discussed renal complications from the use of 
NSAIDs obtained from large population studies (Ref. 20). A study of 
patients 65 years of age and older in the Tennessee Medicaid database 
(Ref. 23) included the following information:
     Eighteen percent of the patients presenting with acute 
renal failure used NSAIDs at either prescription or OTC doses. A RR for 
acute renal failure in NSAID users was calculated to be 1.58 compared 
to NSAID non-users.
     The RR for acute renal failure with ibuprofen was dose 
related. The RR of acute renal failure associated with use of daily 
doses of less than 1,200 mg was approximately 1 compared to use of no 
ibuprofen. Daily doses of 1,200 to 2,400 mg (above the OTC range of 
1,200 mg per day or less) increased the RR of renal failure to 1.89.
     The greatest risk for renal failure was within the first 
30 days of therapy with an NSAID. The RR was 2.83.
    Several drug manufacturers and others provided additional comments 
(Ref. 4). One drug manufacturer stated that the incidence of renal 
failure and other serious renal events are rare with use of either 
prescription or OTC ibuprofen. One drug manufacturer claimed that there 
was an average of approximately five reports of renal failure per year 
from FDA's safety surveillance data. The manufacturers also suggested 
that serious renal events are almost always reversible, even in the 
elderly or chronically ill. It was stated that serious renal events 
following NSAID therapy almost always occur in patients with pre-
existing renal dysfunction, congestive heart failure, or compromised 
hepatic function.
    Several drug manufacturers submitted additional information 
suggesting that (Ref. 5):
     The number of renal side effects that have been reported 
with OTC ibuprofen are minimal (less than two cases of renal failure 
per year), confirming that the drug is well-tolerated.
     The renal safety profile of naproxen/naproxen sodium is 
consistent with other currently marketed NSAIDs with which it has been 
compared. Even at prescription doses, reports of adverse events 
involving the kidney have been rare.
3. NDAC Deliberations and Recommendations Concerning Aspirin and Other 
NSAIDs
     GI bleeding. NDAC members agreed that NSAIDs increase the 
risk for GI adverse events. The risk appears to be related to dose. 
Aspirin, even at lower doses, has some GI risks. However, the benefits 
from use far exceed any risks. NDAC stated that low dose aspirin should 
be available OTC for the elderly for cardiovascular prophylaxis as 
described in the professional labeling. NDAC believed that the absolute 
risk of GI bleeding from use of low dose aspirin is probably comparable 
to the risk from using aspirin at analgesic doses. Therefore, NDAC 
recommended that the information on risk provided in OTC aspirin 
labeling to consumers need not be categorized by dose.
    NDAC agreed that the data support a separate and distinct stomach 
bleeding warning and suggested that the heading ``stomach bleeding 
warning'' be used. NDAC recommended that this heading be in bold type 
and that the warning be included as one of the first warnings in 
labeling along with the Reye's syndrome warning. One NDAC member 
suggested the heading ``bleeding alert'' because aspirin and the other 
NSAIDs can cause more than stomach bleeding, and it is very important 
to stop using an OTC IAAA active ingredient when signs of bleeding are 
present (e.g., vomiting blood or bloody or black stools). Most NDAC 
members felt that stomach bleeding was the major safety problem and 
should be the focus of the warning statement.
    NDAC found that low dose aspirin, combined with another NSAID, will 
increase the risk for GI bleeding two to four times more than use of an 
NSAID alone. From the data reviewed, enteric-coated or buffered aspirin 
preparations do not change the risk associated with use of multiple 
NSAID products. NDAC recommended that the labeling for aspirin and 
other NSAIDs include a stomach bleeding warning advising consumers of 
the risks of taking more than directed or using more than one NSAID. In 
addition, NDAC concluded that the warning should advise consumers that 
the risk is greater for individuals who are over 65 years of age, have 
a history of ulcers, stomach, or bleeding problems, or are taking 
steroids or anticoagulants (blood thinners).
    A majority of NDAC members believed that there were insufficient 
data and a lack of a scientific rationale to support a warning about 
using alcohol while taking NSAIDs. Recognizing that the data are mixed 
and not conclusive, the members believed that a majority of the trials 
reviewed failed to show a direct and convincing association with 
alcohol. NDAC urged FDA to remove the existing alcohol warning from 
labeling and encouraged

[[Page 77328]]

FDA to examine future cases of GI bleeding in individuals who consume 
alcohol and are alcohol abusers to explore the impact of concomitant 
use of NSAIDs.
     Renal effects. NDAC considered particular groups at risk 
for short-term adverse renal consequences from NSAID use. While NDAC 
agreed that small increases in blood pressure of limited duration 
(e.g., several days) in normotensive or hypertensive individuals is not 
a significant risk, the labeling for NSAIDs should warn about the 
potential association of long-term use and renal failure in individuals 
who have high blood pressure, heart or kidney disease, use diuretics, 
or are over 65 years of age. NDAC agreed with the OTC labeling proposed 
for ibuprofen in the Federal Register of August 21, 2002, including the 
warning to ask a doctor before use in the presence of high blood 
pressure, heart or kidney disease, if also using a diuretic, or if over 
65 years of age.
    Labeling. NDAC members agreed that labeling continues to be a major 
factor in promoting the safe and effective use of OTC NSAID products. 
NDAC expressed concern that consumers do not read labels adequately and 
are often unaware of the names of the medicines that they are taking. 
This lack of awareness is especially problematic for people who are 
also taking prescription medicines concomitantly with OTC drug 
products. NDAC expressed concern about the ability to communicate 
meaningful information in the confines of a small package label, 
especially to the elderly. NDAC suggested that patient information be 
included in a package insert to provide expanded information beyond 
what could be presented clearly on a small label.
    NDAC strongly recommend that the term ``NSAID'' be used throughout 
OTC product labeling. The term NSAID is becoming more widely recognized 
and is often found in drug information leaflets. NDAC suggested that 
meaning of the NSAID acronym could be spelled out somewhere on the 
label. Additionally, NDAC recommended that this term should be included 
on the front panel or PDP, advising consumers that the product contains 
an NSAID, especially if the product is a combination containing an 
NSAID. Finally, NDAC members agreed that there is a need for additional 
label comprehension studies to identify ways to improve communication 
with consumers.

IV. FDA's Review of Additional Data and Information

A. Pre-existing Liver Disease as a Risk Factor for Acetaminophen 
Hepatotoxicity

    Following publication of the OTC IAAA TFM in 1988, FDA received 
comments urging adoption of a warning to advise consumers with pre-
existing liver disease against using acetaminophen, unless directed by 
a doctor. The comments cited reports in the medical literature 
concerning toxicity in persons with liver disease. Other comments 
asserted that there is no evidence to warrant a warning. At that time, 
FDA believed the evidence was insufficient to propose a warning. NDAC 
briefly discussed this issue in September 2002, but concluded that 
there were not sufficient data to make specific recommendations.
    FDA has reconsidered its previous position on this issue and now 
believes that the current evidence supports a warning. At the NDAC 
meeting, FDA reported information derived from mortality data of 
acetaminophen overdose (intentional and unintentional). Among patients 
with chronic alcoholic or other chronic liver disease, death associated 
with unintentional acetaminophen overdose was reported far more 
frequently than in association with intentional overdose (see table 4 
of this document). In the series of 282 AERS cases of hepatoxicity 
associated with acetaminophen use presented at the meeting, 70 cases 
were reported as having underlying liver disease.
    Metabolic activation and deactivation are involved in acetaminophen 
elimination (Ref. 25). At a therapeutic dose, the majority (greater 
than 90 percent) of acetaminophen combines with glucuronic acid (the 
major metabolic pathway for adults) and sulfuric acid (the major 
metabolic pathway for children). There is also a second, minor 
metabolic pathway in which a small portion of acetaminophen undergoes 
cytochrome P450 phase I metabolism to the toxic acetaminophen 
metabolite, N-acetyl-p-benzoquinoneimine (NAPQI). This toxic metabolite 
is normally inactivated through combination with hepatic glutathione 
(GSH). Any factors that can change GSH availability (by decreasing 
synthesis and/or increasing utilization or interfering with the 
conjugation enzyme) could potentially influence the hepatotoxicity of 
acetaminophen. Any factors that disturb the balance between these two 
metabolic pathways may affect the amount of acetaminophen metabolized 
by each pathway. After the NDAC meeting, FDA conducted a literature 
review (1966 to January 2003) and determined that the following factors 
may place patients with pre-existing liver disease at a greater risk 
for acetaminophen toxicity (Ref. 26).
     Depletion of hepatic GSH has been found in both alcoholic 
and nonalcoholic liver diseases, suggesting that the diseased liver may 
have less capacity to inactivate the toxic metabolite of acetaminophen. 
(Refs. 27 through 34)
     The hepatic cytochrome P450 enzyme, P450-2E1, metabolizes 
acetaminophen to the toxic metabolite that causes hepatotoxicity. 
Expression of hepatic P450-2E1 tends to increase in stable chronic 
liver diseases.
     Studies have shown that the clearance of acetaminophen 
from the body is impaired in people with chronic liver disease (Refs. 
35, 36, and 37). The disease status of the liver alters drug metabolism 
and drug metabolites made by each metabolic pathway (Refs. 38 and 39).
     In chronic liver disease, hepatic glucuronide and sulfate 
conjugation are decreased (Refs. 40 through 43).
     Significant impairment of total hepatic P450 expression is 
found only in people with severe liver disease (hepatitis with liver 
failure and decompensated cirrhosis) (Ref. 38). Recent studies indicate 
that different types (viral, chemical, or immunological factors) and/or 
states (acute, chronic, or severe) of liver disease selectively 
influence expression of different P450 isozymes.
     Chronic alcohol use significantly induces hepatic P450-2E1 
and increases this enzyme's ability to metabolize acetaminophen to 
NAPQI (Ref. 44). In other types of human liver disease, changes in 
expression and activity of P450-2E1, as well as other P450 isozymes 
(1A2 and 3A4) involved in acetaminophen metabolism, are variable (Refs. 
38, 45, 46, and 47). Both human and animal studies show that hepatic 
P450-2E1 expression is significantly increased in a nonalcoholic fatty 
liver (Refs. 48 and 49).
    Few clinical trials directly assess the hepatotoxicity of 
acetaminophen in people with nonalcoholic liver disease. One double-
blind, placebo controlled, crossover study was conducted in 20 people 
with stable chronic liver disease (including Laennec's cirrhosis, 
alcoholic liver cirrhosis, primary biliary cirrhosis, or chronic 
hepatitis) (Ref. 50). The subjects received 1 g of acetaminophen or 
placebo every 4 hours (a total of 4 g/day) for 13 days. The author 
stated that there were no significant changes in laboratory tests or 
clinical status in the

[[Page 77329]]

acetaminophen and placebo treatments. The author concluded that 
underlying liver disease does not increase patient sensitivity to the 
hepatotoxic effects of acetaminophen at a therapeutic dose. Because of 
the small sample size and crossover study design, FDA believes this 
study is inadequate to make any conclusions regarding the risk for 
acetaminophen hepatotoxicity in patients with chronic liver disease.
    In summary, the single prospective clinical study found by FDA in 
the literature that evaluated the susceptibility of the diseased liver 
to acetaminophen toxicity was not definitive. Analyses of an 
acetaminophen overdose database and a review of the AERS case reports 
suggest, however, that people with a history of liver disease may have 
increased susceptibility to acetaminophen-induced hepatotoxicity. In 
addition, the depletion of hepatic GSH has been found in both alcoholic 
and nonalcoholic liver diseases, suggesting that the diseased liver may 
have less capacity to inactivate the toxic metabolite of acetaminophen. 
Expression of hepatic P450-2E1, a major enzyme for metabolic activation 
of acetaminophen, tends to be increased in stable chronic liver 
diseases, particularly in nonalcoholic fatty liver disease. FDA 
believes that these data collectively establish that it is necessary to 
alert patients with chronic liver disease that they may be at risk for 
developing acetaminophen hepatotoxicity, as an important factor in the 
safe and effective use of acetaminophen products.

B. Updated Literature About Acetaminophen Hepatoxicity

    The Acute Liver Study Group recently published an update of the 
prospective data in patients diagnosed with ALF at 22 tertiary care 
centers. Over a 6-year period from January 1, 1998, to December 31, 
2003, 662 patients fulfilled standard criteria for ALF. Of these cases, 
275 were attributed to acetaminophen hepatotoxicity. The criteria for 
attribution to acetaminophen included one or more of the following: (1) 
A history of potentially toxic acetaminophen ingestion (> 4 g/day) 
within 7 days of presentation; (2) detection of any level of 
acetaminophen in the serum; or (3) a serum alanine aminotransferase 
(ALT) > 1,000 IU/L with a history of acetaminophen ingestion, 
irrespective of acetaminophen level (Ref. 51).
    Of the 275 cases attributed to acetaminophen, the following 
observations were made:
     48% were designated as unintentional injury, 44% were 
designated as an intentional injury and 8% could not be classified to 
either group;
     147 (53%) used an OTC product, including 6 of 147 who used 
more than one OTC product at the same time and 41 of 147 who also used 
a prescription combination product;
     120 (44%) reported use of a narcotic/acetaminophen 
combination;
     55% had a history of alcohol use and 35% had a history of 
alcohol abuse;
     108 (39%) also used a antidepressant;
     65% survived without transplant; and
     22% used more than one acetaminophen product.
    The authors also compared characteristics between those classified 
as unintentional versus intentional liver injury. Females predominate 
in both groups. The clinical outcomes are similar for both groups. 
Narcotic/acetaminophen use was more prevalent in the unintentional 
injury group (63% vs. 18%). The unintentional injury group had a 
greater percentage with stage 3-4 hepatic coma score at admission and 
at peak during the hospitalization. FDA believes that these data 
support the previous NDAC conclusion that acetaminophen hepatotoxicity 
is an important public health consideration and that additional 
labeling is necessary for it to continue to be generally recognized as 
safe and effective.

C. Aspirin and Other NSAIDs

1. GI Bleeding
    Following the NDAC meeting, FDA reviewed additional data and 
information related to the use of OTC NSAIDs and GI bleeding.
     One individual asserted in a citizen petition that 
incomplete information about aspirin reaches consumers and increases 
the danger that aspirin will be misused with serious consequences (Ref. 
52). The citizen petition suggested that additional labeling for 
aspirin should be implemented without delay to state: ``CAUTION: This 
product can cause severe hemorrhaging and should not be taken for more 
than five days except under the supervision of a physician. When used 
for fever, if symptoms persist more than three days, consult a 
physician.''
     NSAIDs are being used by an estimated 17 million Americans 
on a daily basis (Ref. 53). The estimated rate of serious adverse 
events is about 1 percent for clinically significant GI bleeding in the 
first 3 months of use (Ref. 54). NSAID use is so widespread that NSAID-
induced gastropathy has been identified by some as one of the most 
prevalent, serious drug toxicities in the United States (Ref. 55). 
NSAID-associated serious GI complications are estimated to result in 
over 200,000 hospitalizations per year in the United States. Although 
these adverse event rates are for prescription and OTC NSAID 
formulations combined, there is a significant prevalence of OTC NSAID 
use among people presenting to hospitals with upper GI bleeding (Ref. 
56). The rate of consumption of OTC NSAIDs by consumers is estimated to 
be as much as seven times that of prescribed NSAIDs (Ref. 54).
     The American College of Gastroenterology guideline for 
treatment and prevention of NSAID-induced ulcers indicates an increased 
risk of NSAID-associated GI complications for people greater than 60 
years of age (Ref. 56). A United Kingdom (UK) population-based, 
retrospective case-control study evaluated the risk of various NSAIDs 
(Ref. 10). The study reported a RR of 3.7 for upper GI bleeding (UGIB) 
and GI perforation in people under 60 years old exposed to NSAIDs, 13.2 
in people 60 years and older exposed to NSAIDs, and 2.8 in people 60 
years and older not exposed to NSAIDs.
     FDA analyzed a series of studies that used the Medicaid 
population in Tennessee (Refs. 12, 13, 56, 57, and 58). These case-
controlled retrospective studies were based on hospitalizations for GI 
bleeds. The study population totaled 103,954 individuals, about 15 
percent of Tennessee's elderly population, with 209,066 person-years of 
followup. There were 1,371 hospitalizations for PUD. These studies 
found increased risk of GI bleeds in people who were:
     Over 65 years old (RR of 4.7),
     Taking an increased NSAID dose (RR of 2.8 for the lowest 
dose vs. RR of 8 for the highest dose category), or
     Taking concomitant corticosteroid (RR of 4.4) or anti-
coagulant (RR 12.7) drug products.
    In addition, the risk of GI bleeds among people taking NSAIDs was 
greatest within the first 30 days of use (RR of 7.2).
     A multicenter, case-control study of 550 people with UGIB 
admitted to a hospital with bloody stools or vomiting blood and 1,202 
controls identified from census lists, compared risks of major GI 
bleeding for plain, coated, and buffered formulations of low-dose 
aspirin (Ref. 59). Each of these types of low-dose aspirin formulations 
(less than 325 mg

[[Page 77330]]

per day) had about a 2.5 to 3 times increased risk of major UGIB.
     A double-blind, randomized, placebo-controlled, ulcer 
prevention study in 8,843 people with rheumatoid arthritis identified 
several risk factors for upper GI complications from NSAID use: (1) Age 
75 years or older (odds ratio 2.48), (2) prior peptic ulcer (odds ratio 
2.29), (3) prior GI bleeding (odds ratio 2.56), and (4) history of 
cardiovascular disease (odds ratio 1.84) (Ref. 60).
     A case control study of 1,122 subjects admitted 
consecutively for UGIB to four hospitals in Spain and 2,231 controls 
from the same geographic area, showed that a prior history of UGIB is a 
risk factor (odds ratio 3.7) for UGIB in people who used NSAIDs (Ref. 
61).
    In summary, results of several large-scale clinical studies, 
conducted in the United States and worldwide, have established that use 
of OTC NSAIDs is an important risk factor for serious GI adverse 
events, especially bleeding. The risk is higher for people age 60 or 
older, who have a history of stomach ulcers or bleeding problems, or 
who use corticosteroids or anticoagulants.
2. Renal Effects
    NSAIDs decrease renal prostaglandin production, which may result in 
acute reduction in renal blood flow and glomerular filtration, leading 
to fluid retention, edema, and elevation of serum creatinine (Ref. 62). 
Marked reduction in renal blood flow may result in renal failure.
    NSAID use may also result in higher than normal levels of potassium 
in the bloodstream. This occurs most commonly in people with diabetes 
mellitus or mild to moderate renal insufficiency as well as in people 
taking beta-blocker, angiotensin-converting enzyme inhibitor, or 
potassium-sparing diuretic drugs.
    By inhibiting the production of vasodilatory prostaglandins, NSAIDs 
may decrease renal blood flow and the rate of glomerular filtration in 
subjects with congestive heart failure, liver failure with ascites, 
chronic renal disease, or those who are hypovolemic (abnormal volume 
decrease of circulating fluid (plasma) in the body) (Refs. 63, 64, and 
65).
    a. Pediatric population. The medical literature includes sporadic 
reports of acute renal failure in pediatric subjects taking ibuprofen 
within the OTC dose range, including the following cases:
     One article describes three cases in children 5-, 6.5-, 
and 7.5-years-old in which ibuprofen treatment led to varying degrees 
of renal failure (Ref. 66). Two subjects with dehydration and pre-
existing renal problems were prescribed ibuprofen for the treatment of 
fever due to acute illness. Both had a recovery of renal function on 
withdrawal of the drug. The third child (a 7.5-year-old girl) developed 
progressive chronic renal failure. She had underlying hyper Ig-E 
syndrome and was treated with a single dose of ibuprofen 5 mg /kg for 
fever due to severe pulmonary infection. Her illness was also 
complicated by moderate dehydration. Her renal biopsy showed evidence 
of kidney damage consistent with loss of blood circulation.
     Ibuprofen-induced acute renal failure was reported in a 9-
month-old girl (Ref. 67). A family practitioner treated the infant for 
diarrhea, vomiting, and fever. She was given oral rehydration therapy 
and acetaminophen and was sent home. Symptoms persisted for 48 hours 
and the acetaminophen was changed to ibuprofen 50 mg (5 mg/kg/dose) 
three times a day. Seven doses of ibuprofen were given over a 40-hour 
period, but the child's clinical state deteriorated. She was admitted 
to an emergency facility 18 hours after the last dose with a creatinine 
concentration of 2.1 mg/deciliter (dL). For the first 12 hours after 
admission, the infant's kidneys failed to secrete urine in spite of 
receiving adequate hydration and an intravenous diuretic (furosemide). 
The creatinine concentration increased to 2.4 mg/dL. Renal function 
slowly recovered; 4 days after admission her creatinine was 0.9 mg/dL 
and 3 weeks later was 0.5 mg/dL. Clinical diagnosis was kidney damage 
secondary to ibuprofen use in a dehydrated child.
     Primack, et al. reported acute renal failure with use of 
ibuprofen in an 11-year-old boy (Ref. 68). The child was diagnosed with 
possible sinusitis and given an antibiotic; on the third day symptoms 
worsened with associated headaches, fatigue and anorexia, and his serum 
creatinine was 0.7 mg/dL. The antibiotic was continued and ibuprofen 
200 mg was added, alternating with acetaminophen every 4 hours for 
fever. He received a total of 24 200-mg ibuprofen tablets during the 12 
days prior to hospitalization. The fever persisted with improvement in 
the other symptoms. The child became progressively weaker and began 
vomiting. Approximately 2 weeks after his illness began, the child was 
admitted with a serum creatinine of 7.6 milliequivalent/L. After 3 days 
of symptomatic treatment, his serum creatinine was 4.1 mg/dL and 1 week 
later his serum creatinine was 2.2 mg/dL. Findings of renal biopsy on 
the third hospital day were consistent with acute interstitial 
nephritis, which the authors attributed to beta-lactam antibiotic use.
    These case reports demonstrate the variety of situations in which 
ibuprofen-associated renal toxicity can occur. In many of the cases, 
the children were already at risk for renal adverse effects because of 
underlying disease states, concomitant medications, or dehydration. 
Children with underlying illnesses or those dehydrated are at greatest 
risk for this injury. FDA currently requires all OTC pediatric products 
containing ibuprofen marketed under new drug applications to include 
warnings for children ages 2 to 11 years to ask a doctor before use if 
the child has ``not been drinking fluids'' or has ``lost a lot of fluid 
due to continued vomiting or diarrhea.''
    b. Alcohol use. Binge drinking of alcohol reduces the production of 
antidiuretic hormone causing increased urine production. Two cases of 
reversible acute deterioration in renal function following binge 
drinking of beer with use of NSAIDs have been reported in adults (Ref. 
69):
     The authors reported a case of a 22-year old male admitted 
to the hospital with low back pain and worsening renal function. Four 
days prior to admission, he had consumed an unknown amount of beer; 2 
days later as the pain intensified he had taken six doses of 400-mg 
ibuprofen with no relief. Upon admission, his serum creatinine was 3.1 
mg/dL. Biopsy of the kidney was consistent with the diagnosis of acute 
kidney failure. The subject's serum creatinine increased to a peak of 
6.5 mg/dL on the fourth day and decreased to 1.4 mg/dL 6 days later.
     In a second case, a 20-year old male was admitted because 
of flank and back pain of 24 hours' duration. Four days before 
admission, the subject drank 8 to 10 bottles of beer (355 mL per 
bottle). On the evening of admission, he had taken 6 to 8 tablets of 
325-mg aspirin for pain relief. The laboratory data showed a 2.0 mg/dL 
serum creatinine level. Following intravenous fluid administration, the 
subject urinated frequently for over 16 hours. Followup serum 
creatinine 1 week later was 1.2 mg/dL. The authors concluded that 
dehydration is a frequent consequence of heavy alcohol ingestion due to 
water diuresis. The volume contraction may be further aggravated by 
nausea and vomiting.
    In the proposed rule to amend the TFM for OTC IAAA drug products to 
include ibuprofen, FDA included the results of the agency's evaluation 
of the adverse renal effects of OTC doses of ibuprofen (67 FR 54139 at 
54144). Based on its evaluation of the data, FDA

[[Page 77331]]

concluded that OTC doses of ibuprofen can exert a variety of adverse 
renal effects, particularly in those who are dependent on adequate 
prostaglandin levels to maintain renal hemodynamic perfusion (i.e., 
congestive heart failure, liver failure with ascites, etc.). It was 
further noted that although the sporadic nature of idiosyncratic drug-
induced ibuprofen nephrotoxicity makes it impossible to predict which 
group of individuals is at risk for developing this event, this is not 
the case with individuals who experience prostaglandin-dependent 
hemodynamic changes. The latter, if recognized, is reversible upon 
discontinuation of the drug (67 FR 54139 at 54145).

V. FDA's Tentative Conclusions

    FDA has carefully considered NDAC's recommendations and other 
available data and information and determined that labeling revisions 
are necessary for OTC IAAA drug products to advise consumers of 
potential health risks and to recommend, under certain circumstances, 
that they consult a doctor for advice about taking products containing 
OTC IAAA active ingredients.
    FDA continues to believe that acetaminophen and NSAIDs, when 
labeled appropriately and used as directed, are generally recognized as 
safe and effective OTC IAAA drugs for consumer self-use. However, the 
available evidence clearly indicates that both drugs can cause serious 
side effects. When taken in excess amounts, acetaminophen can cause 
liver injury. NSAIDs have the potential to cause GI bleeding and renal 
(kidney) injury even at OTC dosing levels.
    When compared to the extensive use of OTC acetaminophen and NSAID 
drug products, the incidence of injury appears relatively low. However, 
based on the available evidence and the seriousness of the risks, FDA 
believes it is necessary for consumers to be made aware of the possible 
serious side effects associated with using these products. For many 
people, the risks are quite low because they use these products only 
occasionally. The risks may be greater for people who use these 
products more frequently, have certain risk factors, and/or do not 
follow the labeling information on the package. FDA believes that 
providing additional labeling information about how to correctly use 
OTC drug products containing acetaminophen and NSAIDs could reduce 
injuries and is necessary for the products to be considered generally 
recognized as safe and effective and not misbranded.
    FDA plans to act on several fronts:
     Propose revised OTC labeling for these products
     Continue a consumer and health provider educational 
campaign
     Continue to monitor AERS in various databases
     Examine available data to determine whether other measures 
may be needed in the future to try to decrease morbidity associated 
with OTC acetaminophen and NSAIDs.
    In addition to the changes to the IAAA TFM proposed in this 
document, FDA encourages manufacturers of these products to undertake 
education initiatives regarding safe use of OTC products containing 
acetaminophen and NSAIDs. FDA plans to increase its monitoring of AERS 
in various databases to see how this new proposed labeling, if 
implemented, is working to reduce injuries resulting from OTC 
acetaminophen and NSAID drug products and to determine whether further 
measures need to be proposed.

A. Acetaminophen

1. Hepatotoxicity
    FDA tentatively concludes that additional new labeling is needed 
for OTC drug products that contain acetaminophen. Data from Lee (Ref. 
6), a case series from the University of Pennsylvania Hospital (Ref. 
4), and the FDA AERS database show that unintentional overuse of 
acetaminophen is associated with severe hepatic injury. One 
manufacturer provided calculations of a ``worst case'' scenario for 
acetaminophen hepatic failure deaths using estimates by Lee (Ref. 70) 
and calculated 213 deaths per year. FDA does not know the exact number 
of cases of liver failure or deaths related to unintentional 
acetaminophen overdose. FDA thinks that improved labeling may help 
prevent events that are catastrophic to the unintentional victims and 
their family members. FDA has determined that adding a liver warning is 
necessary for safe and effective use of the drug and to reduce the 
number of unintentional overdoses. Thus, FDA is proposing a ``liver 
warning'' stating use factors that could lead to liver injury.
    FDA notes that NDAC recommended both an alcohol warning and a liver 
toxicity statement separate from the alcohol warning for OTC drug 
products containing acetaminophen. FDA has combined this information 
because it is interrelated and a shorter warning saves label space on 
products that already contain extensive labeling information. FDA 
believes that two, separate warnings may be less likely to be read and 
understood by consumers.
    FDA also tentatively concludes that a new warning is needed to 
advise consumers who have liver disease to consult a doctor before 
using OTC drug products that contain acetaminophen. FDA notes that many 
of the case reports in the databases involved people who had pre-
existing liver disease (the rate of the number of cases in the 
databases exceeds the rate of underlying liver disease in the general 
population). This observation may also be due to a difference in the 
use of acetaminophen by people with chronic liver disease or that they 
are at greater risk to develop liver failure in general. As described 
in section IV.A of this document, people with chronic liver disease can 
have changes in the liver enzymes responsible for the metabolism of 
acetaminophen. It is not clear whether these changes increase the risk 
in these individuals. It was noted at NDAC that some physicians who 
treat patients with chronic liver disease recommend lower total daily 
doses. FDA believes this additional warning will alert patients with 
chronic liver disease to ask their doctor before using acetaminophen. 
FDA recognizes there is limited information supporting the need for 
different dose recommendations in people with liver disease. FDA seeks 
comment on the information this warning should provide and encourages 
healthcare providers and researchers who treat patients with chronic 
liver disease to prov